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NCT01353430
- Conditions
- Bone Diseases, Brain Diseases, Central Nervous System Diseases, +19 more
- Locations
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- University of California, Irvine Irvine, California, United States
Recruiting
Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
NCT01793168
- Conditions
- 1p36 Deletion Syndrome, 3-Methylglutaconic Aciduria, Type V, 4p Deletion Syndrome, Non-Wolf-Hirschhorn Syndrome, +698 more
- Locations
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- Sanford Health Sioux Falls, South Dakota, United States
- Online Patient Enrollment System Sydney, Australia
NCT04823143
- Conditions
- IBMPFD, Inclusion Body Myopathy With Early-Onset Paget Disease And Frontotemporal Dementia
- Locations
-
- Nationwide Children's Hospital Columbus, Ohio, United States
NCT04060082
- Conditions
- Brain Diseases, Central Nervous System Diseases, Dementia, +16 more
- Locations
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- Johns Hopkins Medical Institution Baltimore, Maryland, United States
- National Institutes of Health (NIH) Bethesda, Maryland, United States
- University of Pennsylvania (Penn Frontotemporal Degeneration Center) Philadelphia, Pennsylvania, United States