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NCT01861106
- Conditions
- Anemia, Anemia, Refractory, Anemia, Refractory, with Excess of Blasts, +9 more
- Locations
-
- National Institutes of Health Clinical Center Bethesda, Maryland, United States
Recruiting
Genetic Analysis of Immune Disorders
NCT00001467
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DOK 8, GATA2, +7 more
- Locations
-
- National Institutes of Health Clinical Center Bethesda, Maryland, United States
NCT05027945
- Conditions
- Autoimmune Diseases, Bone Marrow Diseases, Hematologic Diseases, +6 more
- Locations
-
- National Institutes of Health Clinical Center Bethesda, Maryland, United States
NCT06839456
- Conditions
- Acquired Aplastic Anemia, Anemia, Anemia, Refractory, +35 more
- Locations
-
- Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
NCT04408950
- Conditions
- Immune System Diseases, Immunodeficiency, Immunologic Deficiency Syndromes
- Locations
-
- National Institutes of Health Clinical Center Bethesda, Maryland, United States
Completed
Pilot and Feasibility Study of Reduced-Intensity Hematopoietic Stem Cell Transplant for MonoMAC
NCT00923364
- Conditions
- Anemia, Anemia, Refractory, Anemia, Refractory, with Excess of Blasts, +12 more
- Locations
-
- National Institutes of Health Clinical Center, 9000 Rockville Pike Bethesda, Maryland, United States
- Conditions
- Immune System Diseases, Immunodeficiency, Immunologic Deficiency Syndromes
- Locations
-
- St. Jude Children's Research Hospital Memphis, Tennessee, United States
NCT00925925
- Conditions
- Immune System Diseases, Immunodeficiency, Immunologic Deficiency Syndromes, +2 more
- Locations
-
- University of Utah Salt Lake City, Utah, United States
Active, Not Recruiting
Allogeneic Hematopoietic Stem Cell Transplantation With Briquilimab-Based Conditioning in Participants With GATA2 Deficiency
NCT05907746
- Conditions
- GATA2, Immune System Diseases, Immunodeficiency, +1 more
- Locations
-
- National Institutes of Health Clinical Center Bethesda, Maryland, United States