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Enrolling by Invitation
Registry of Patients With Hypophosphatasia
NCT02306720
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Hypophosphatasia, +5 more
- Locations
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- Research Site Centennial, Colorado, United States
- Research Site Hartford, Connecticut, United States
- Research Site Tampa, Florida, United States
- Research Site Decatur, Georgia, United States
NCT01419028
- Conditions
- Avitaminosis, Bone Diseases, Bone Diseases, Metabolic, +16 more
- Locations
-
- Cedars-Sinai Medical Center Los Angeles, California, United States
- Indiana University school of medicine Indianapolis, Indiana, United States
- Shriners Hospital for Children St Louis, Missouri, United States
- Oregon Health & Science University Portland, Oregon, United States
NCT02104219
- Conditions
- Avitaminosis, Bone Diseases, Bone Diseases, Metabolic, +16 more
- Locations
-
- Atlanta, Georgia, United States
- Indianapolis, Indiana, United States
- Boston, Massachusetts, United States
- Springfield, Missouri, United States
Completed
Safety and Efficacy Study of Asfotase Alfa in Severely Affected Infants With Hypophosphatasia (HPP)
NCT00744042
- Conditions
- Avitaminosis, Bone Diseases, Bone Diseases, Metabolic, +16 more
- Locations
-
- Arkansas Children's Hospital Little Rock, Arkansas, United States
- Alfred I. duPont Hospital for Children Wilmington, Delaware, United States
- St. John's Hospital Springfield, Missouri, United States
- University of Nebraska Medical Center, Munroe-Meyer Institute Omaha, Nebraska, United States
NCT00952484
- Conditions
- Avitaminosis, Bone Diseases, Bone Diseases, Metabolic, +16 more
- Locations
-
- Shriners Hospital for Children St Louis, Missouri, United States
- The University of Manitoba Health Services Centre Winnipeg, Manitoba, Canada
NCT00739505
- Conditions
- Avitaminosis, Bone Diseases, Bone Diseases, Metabolic, +16 more
- Locations
-
- Barnes Jewish Hospital- Washington University School of Medicine St Louis, Missouri, United States
- Duke University Medical Center Durham, North Carolina, United States
- Department of Pediatrics & Child Health, Health Sciences Centre Winnipeg, University of Manitoba Winnipeg, Manitoba, Canada
NCT01203826
- Conditions
- Avitaminosis, Bone Diseases, Bone Diseases, Metabolic, +16 more
- Locations
-
- Shriners Hospital for Children St Louis, Missouri, United States
- Children's Hospital Health Sciences Centre Winnipeg, Manitoba, Canada