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Published and searchable clinical trials
NCT02237625
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Hypophosphatasia, +4 more
- Locations
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- Duke University Medical Center Durham, North Carolina, United States
NCT05234567
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Hypophosphatasia, +4 more
- Locations
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- Clinical Trial Site Hartford, Connecticut, United States
- Clinical Trial Site Chicago, Illinois, United States
- Clinical Trial Site Boston, Massachusetts, United States
- Clinical Trial Site Kansas City, Missouri, United States
NCT07179640
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Hypophosphatasia, +5 more
- Locations
-
- New Zealand Clinical Research Grafton, Auckland, New Zealand
- Fortrea Clinical Research Unit Leeds, United Kingdom
Prospective, Longitudinal, Observational Registry of Adult Patients With Hypophosphatasia (REG-HYPO)
NCT05596539
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Enthesopathy, Genetic Diseases, Inborn, +10 more
- Locations
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- CHU de Bordeaux- Hôpital Pellegrin Place Amélia Raba Léon - 12è étage - Rhumatologie - Bordeaux, France
- CHU Lille Lille, France
- Hospices Civils de Lyon Lyon, France
- CHU Nice Nice, France
Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
NCT01793168
- Conditions
- 1p36 Deletion Syndrome, 3-Methylglutaconic Aciduria, Type V, 4p Deletion Syndrome, Non-Wolf-Hirschhorn Syndrome, +698 more
- Locations
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- Sanford Health Sioux Falls, South Dakota, United States
- Online Patient Enrollment System Sydney, Australia
NCT06574282
- Conditions
- Bone Diseases, Bone Diseases, Metabolic, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +11 more
- Locations
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- Clinic of Internal Medicine III, Department of Oncology, Haematology, Rheumatology and Clinical Immunology, University Hospital Bonn Bonn, North Rhine-Westphali, Germany
Registry of Patients With Hypophosphatasia
NCT02306720
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Hypophosphatasia, +5 more
- Locations
-
- Research Site Centennial, Colorado, United States
- Research Site Hartford, Connecticut, United States
- Research Site Tampa, Florida, United States
- Research Site Decatur, Georgia, United States
GRACE II (General Retrospective Analysis of Commercial Experience With AGN1 LOEP)
NCT07594639
- Conditions
- Bone Diseases, Bone Diseases, Developmental, Bone Diseases, Metabolic, +20 more
- Locations
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- Vitaz Sint-Niklaas, Belgium
NCT05062629
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Hypophosphatasia, +4 more
- Locations
-
- Children's Mercy Hospital Kansas City, Missouri, United States
NCT05890794
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Hypophosphatasia, +4 more
- Locations
-
- Osteologie / Klinische Studieneinheit, Orthopädische Klinik - KLH Würzburg, Germany
NCT04980248
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Hypophosphatasia, +4 more
- Locations
-
- Research Site Las Vegas, Nevada, United States
- Research Site Columbus, Ohio, United States
- Research Site Nashville, Tennessee, United States
- Research Site Austin, Texas, United States
NCT06689709
- Conditions
- Alkaline Phosphatase Deficiency, Avitaminosis, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +10 more
- Locations
-
Not specified
NCT04195763
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Hypophosphatasia, +4 more
- Locations
-
- Xcenda, LLC Palm Harbor, Florida, United States
NCT02796885
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Hypophosphatasia, +4 more
- Locations
-
- Nuffield Orthopaedic Research Oxford, United Kingdom
- University of Sheffield Sheffield, United Kingdom
NCT01406977
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Hypophosphatasia, +4 more
- Locations
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- Mereo BioPharma 3 Ltd Investigative Site Würzburg, Germany
Evaluate and Monitor Physical Performance of Adults Treated With Asfotase Alfa for Hypophosphatasia
NCT03418389
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Hypophosphatasia, +4 more
- Locations
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- Clinical Trial Unit, Orthopedic Department, Wuerzburg University Würzburg, Germany
NCT04925804
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Hypophosphatasia, +4 more
- Locations
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- Universität Würzburg - Klinische Studieneinheit, Orthopädische Klinik Würzburg, Germany
NCT02797821
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Hypophosphatasia, +4 more
- Locations
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- Shriners Hospitals for Children St Louis, Missouri, United States
- Duke University Medical Center Durham, North Carolina, United States
- Vanderbilt Medical Center Endocrinology Nashville, Tennessee, United States
- University of Würzburg Würzburg, Germany
NCT01419028
- Conditions
- Avitaminosis, Bone Diseases, Bone Diseases, Metabolic, +16 more
- Locations
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- Cedars-Sinai Medical Center Los Angeles, California, United States
- Indiana University school of medicine Indianapolis, Indiana, United States
- Shriners Hospital for Children St Louis, Missouri, United States
- Oregon Health & Science University Portland, Oregon, United States
NCT02104219
- Conditions
- Avitaminosis, Bone Diseases, Bone Diseases, Metabolic, +16 more
- Locations
-
- Atlanta, Georgia, United States
- Indianapolis, Indiana, United States
- Boston, Massachusetts, United States
- Springfield, Missouri, United States