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Showing 1–12 of 12 trials
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Published and searchable clinical trials
NCT06410976
- Conditions
- Bone Diseases, Bone Diseases, Developmental, Carbohydrate Metabolism, Inborn Errors, +16 more
- Locations
-
- UCSF Benioff Children's Hospital Oakland, California, United States
- Childrens Hospital Colorado Aurora, Colorado, United States
- Children's National Hospital Washington D.C., District of Columbia, United States
- Johns Hopkins School of Medicine Baltimore, Maryland, United States
A Study of Vosoritide Versus Placebo in Children With Hypochondroplasia Aged 0 to < 36 Months
NCT07126262
- Conditions
- Hypochondroplasia
- Locations
-
- Phoenix Children's Hospital - Thomas Campus (Main) Phoenix, Arizona, United States
- Cedars-Sinai Medical Center Los Angeles, California, United States
- Benioff Children's Hospital - Oakland Oakland, California, United States
- Children's National Medical Center Washington D.C., District of Columbia, United States
NCT07388966
- Conditions
- Achondroplasia, Bone Diseases, Bone Diseases, Developmental, +6 more
- Locations
-
- Hopital Necker Paris, France
NCT06212947
- Conditions
- Hypochondroplasia
- Locations
-
- Phoenix Children's Hospital Phoenix, Arizona, United States
- Cedars-Sinai Medical Center Los Angeles, California, United States
- UCSF Benioff Children's Hospital Oakland, California, United States
- Nemours Alfred I. Dupont Hospital for Children Wilmington, Delaware, United States
NCT05328050
- Conditions
- Achondroplasia, Bone Diseases, Bone Diseases, Developmental, +6 more
- Locations
-
- Medical Genetics Unit, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico Milan Milan, Italy
An Interventional Study of Infigratinib in Children With Hypochondroplasia
NCT06873035
- Conditions
- Bone Diseases, Bone Diseases, Developmental, Carbohydrate Metabolism, Inborn Errors, +16 more
- Locations
-
- UCSF Benioff Children's Hospital Oakland, California, United States
- Childrens Hospital Colorado Aurora, Colorado, United States
- Children's National Hospital Washington D.C., District of Columbia, United States
- Johns Hopkins School of Medicine Baltimore, Maryland, United States
Open-Label, Long-Term, Extension Study of Infigratinib in Children With Hypochondroplasia
NCT07393373
- Conditions
- Bone Diseases, Bone Diseases, Developmental, Carbohydrate Metabolism, Inborn Errors, +16 more
- Locations
-
- UCSF Benioff Children's Hospital Oakland, California, United States
- Childrens Hospital Colorado Aurora, Colorado, United States
- Children's National Hospital Washington D.C., District of Columbia, United States
- Johns Hopkins School of Medicine Baltimore, Maryland, United States
Long-Term Extension Study of Vosoritide to Treat Children With Hypochondroplasia
NCT07073014
- Conditions
- Hypochondroplasia
- Locations
-
- Nemours Children's Hospital, Delaware (Alfred I. Dupont Hospital for Children) Wilmington, Delaware, United States
- Children's National Medical Center Washington D.C., District of Columbia, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- Medical College of Wisconsin Milwaukee, Wisconsin, United States
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
- Locations
-
- Endocrinologie Pédiatrique - centre des maladies rares de la croissance -Hôpital Necker Enfants Malades Paris, France
NCT01541306
- Conditions
- Achondroplasia, Bone Diseases, Bone Diseases, Developmental, +7 more
- Locations
-
- Alfred I. duPont Hospital for Children Wilmington, Delaware, United States
Vosoritide for Selected Genetic Causes of Short Stature
NCT04219007
- Conditions
- Bone Diseases, Bone Diseases, Developmental, Cardiovascular Abnormalities, +16 more
- Locations
-
- Children's National Hospital Washington D.C., District of Columbia, United States
Interventional Study of Vosoritide for the Treatment of Children With Hypochondroplasia
NCT06455059
- Conditions
- Bone Diseases, Bone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +6 more
- Locations
-
- Nemours Alfred I. DuPont Hospital for Children Wilmington, Delaware, United States
- Children's National Medical Center Washington D.C., District of Columbia, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- Medical College of Wisconsin Milwaukee, Wisconsin, United States