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Published and searchable clinical trials
NCT06255782
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +19 more
- Locations
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- UCLA Mattel Children's Hospital Los Angeles, California, United States
- Children's Hospital of Colorado, Anshutz Medical Campus Aurora, Colorado, United States
- Emory University School of Medicine Atlanta, Georgia, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
An Observational Study of Carbaglu® for the Treatment of MMA and PA in Adults and Pediatrics
NCT05040178
- Conditions
- Amino Acid Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +9 more
- Locations
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- Children's National Hospital Washington D.C., District of Columbia, United States
- University of South Florida Tampa, Florida, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- Riley Children's Hospital Indianapolis, Indiana, United States
NCT06805695
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +18 more
- Locations
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- Great Ormond Street Hospital London, United Kingdom
International Registry of Congenital Portosystemic Shunt (IRCPSS)
NCT06041906
- Conditions
- 46, XX Disorders of Sex Development, Adrenogenital Syndrome, Brain Diseases, +45 more
- Locations
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- Yale University School of Medicine New Haven, Connecticut, United States
- Lurie Children's Hospital Chicago, Illinois, United States
- Royal Children's Hospital Melbourne Parkville, Victoria, Australia
- Universitary Clinics Saint-Luc, UCL Brussels, Belgium
NCT06135675
- Conditions
- Hyperammonemia, Pathologic Processes, Pathological Conditions, Signs and Symptoms
- Locations
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- The First Hospital of Jilin University Changchun, Jilin, China
A Phase 1 Study to Evaluate PK Profile and Food Effects on PK Parameters of TNP-2092 Capsules
NCT06178718
- Conditions
- Hyperammonemia, Pathologic Processes, Pathological Conditions, Signs and Symptoms
- Locations
-
- The First Hospital of Jilin University Changchun, Jilin, China
Non-Cirrhotic Hyperammonemia Versus Hyperlactatemia in Septic Patients and Impact of Treatment
NCT06721845
- Conditions
- Hyperammonemia, Infections, Inflammation, +4 more
- Locations
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- Menoufia Faculty of Medicine Shibin Elkoom, Menoufia, Egypt
To Evaluate the Safety of Long-term Use of HPN-100 in the Management of Urea Cycle Disorders (UCDs)
NCT01257737
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +13 more
- Locations
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- UCLA Pediatrics/Genetics Los Angeles, California, United States
- Stanford University School of Medicine Palo Alto, California, United States
- Denver Children's Hospital Aurora, Colorado, United States
- Children's National Medical Center Washington D.C., District of Columbia, United States
NCT00947544
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +13 more
- Locations
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- UCLA Los Angeles, California, United States
- The George Washington DC Children's National Medical Center Washington D.C., District of Columbia, United States
- Mount Sinai School of Medicine New York, United States
- University of Pittsburgh Pittsburgh, Pennsylvania, United States
NCT01347073
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +13 more
- Locations
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- UCLA Pediatrics/Genetics Los Angeles, California, United States
- Children's National Medical Center Washington D.C., District of Columbia, United States
- Maine Medical Center Portland, Maine, United States
- University of Minnesota Minneapolis, Minnesota, United States
NCT00947297
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +13 more
- Locations
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- Long Beach Memorial Long Beach, California, United States
- UCLA Los Angeles, California, United States
- Stanford University Stanford, California, United States
- Children's Hospital Colorado Aurora, Colorado, United States
NCT00992459
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +13 more
- Locations
-
- Long Beach Memorial Long Beach, California, United States
- UCLA Los Angeles, California, United States
- Stanford University Stanford, California, United States
- Denver Children's Hospital Aurora, Colorado, United States
NCT02246218
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +13 more
- Locations
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- Kaiser Permanente Regional Metabolic Center Los Angeles, California, United States
- Stanford Center for Clinical & Translational Research & Education Palo Alto, California, United States
- Children's National Medical Center Washington D.C., District of Columbia, United States
- Shands at University of Florida Gainesville, Florida, United States
NCT01569568
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +15 more
- Locations
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Not specified
NCT03947034
- Conditions
- Adverse Drug Event, Chemically-Induced Disorders, Drug Toxicity, +7 more
- Locations
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- AP-HP, Pitié-Salpêtrière Hospital, Department of Pharmacology, CIC-1421, Pharmacovigilance Unit, INSERM Paris, France
NCT03797222
- Conditions
- Glucose Metabolism Disorders, Hyperammonemia, Hyperinsulinemic hypoglycemia, familial, 6, +7 more
- Locations
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- Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
NCT01966419
- Conditions
- Acute Episode of Overt Hepatic Encephalopathy, Brain Diseases, Brain Diseases, Metabolic, +13 more
- Locations
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- Phoenix, Arizona, United States
- Phoenix, Arizona, United States
- Little Rock, Arkansas, United States
- Coronado, California, United States
NCT01599286
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +21 more
- Locations
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- University of California Los Angeles Los Angeles, California, United States
- Lucile Packard Children's Hospital at Stanford Palo Alto, California, United States
- The Children's Hospital of Colorado Aurora, Colorado, United States
- Children's National Medical Center Washington D.C., District of Columbia, United States
NCT01624311
- Conditions
- Amino Acid Metabolism, Inborn Errors, Argininosuccinic Aciduria, Brain Diseases, +31 more
- Locations
-
- Children's National Medical Center Washington D.C., District of Columbia, United States
- Columbia University, Morgan Stanley Children's Hospital New York, United States
- Medical College Wisconsin Milwaukee, Wisconsin, United States
NCT00645879
- Conditions
- Amino Acid Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +12 more
- Locations
-
- University of Utah, Department of Pediatrics Salt Lake City, Utah, United States