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Published and searchable clinical trials
NCT03513328
- Conditions
- Acquired Anemia Hemolytic, Acquired Neutropenia in Newborn, Acquired Thrombocytopenia, +82 more
- Locations
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- UF Health Shands Children's Hospital Gainesville, Florida, United States
NCT01173016
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
- Locations
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- Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States
NCT01917708
- Conditions
- Albinism, Anemia, Anemia, Aplastic, +80 more
- Locations
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- Children's Healthcare of Atlanta Atlanta, Georgia, United States
Neurobehavioral Phenotypes in MPS III
NCT01873911
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Cognition Disorders, Cognitive Dysfunction, +17 more
- Locations
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- University of Minnesota Minneapolis, Minnesota, United States
NCT00176891
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
- Locations
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- Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States
NCT00638547
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
- Locations
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- University of Minnesota, Fairview Minneapolis, Minnesota, United States
NCT01043640
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +52 more
- Locations
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- Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States
NCT00146757
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +12 more
- Locations
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- Hôpital E. Herriot Lyon, France
- Johannes Gutenberg Universität Kinderklinik, Mainz, Germany
- Sophia Children's Hospital Rotterdam, Netherlands
- Willink Biochemical Genetics Unit Royal Hospital for Children Manchester, United Kingdom
Study of Aldurazyme® Replacement Therapy in Patients With Mucopolysaccharidosis I (MPS I) Disease
NCT00258011
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +12 more
- Locations
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- Osaka City University Hospital Osaka, Japan
- National Center for Child Health and Development Tokyo, Japan
MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis
NCT02171104
- Conditions
- Abnormalities, Multiple, Acyl-CoA Oxidase Deficiency, Adrenoleukodystrophy With Cerebral Involvement, +85 more
- Locations
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- Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States