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RGX-121-3102 Gene Therapy in Participants With MPS II (Hunter Syndrome)
NCT07236606
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +24 more
- Locations
-
- St. Peter's University Hospital New Brunswick, New Jersey, United States