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Published and searchable clinical trials
NCT02455622
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +17 more
- Locations
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- Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- Hospital Infantil Dr Robert Reid Cabral Santo Domingo, Dominican Republic
- Universitätsmedizin der Johannes Gutenberg-Universität Mainz Mainz, Germany
- Hospital Kuala Lumpur Kuala Lumpur, Malaysia
An Extension Study to Assess the Long-term Safety and Efficacy of Hunterase (Idursulfase Beta)
NCT07344376
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +27 more
- Locations
-
- Samsung Medical Center Seoul, South Korea
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +23 more
- Locations
-
- Ann & Robert H Lurie Childrens Hospital of Chicago Chicago, Illinois, United States
- University of North Carolina at Chapel Hill Chapel Hill, North Carolina, United States
- Legacy Emanuel Hospital Portland, Oregon, United States
- Children's Hospital of Pittsburgh of UPMC Pittsburgh, Pennsylvania, United States
NCT02412787
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +17 more
- Locations
-
- Children's Hospital and Research Center at Oakland Oakland, California, United States
- Ann & Robert H Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- University of North Carolina Chapel Hill, North Carolina, United States
- Women's and Children's Hospital Adelaide, Australia
A Study of Elaprase in Children and Adults With Hunter Syndrome (Mucopolysaccharidosis II) in India
NCT05058391
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +17 more
- Locations
-
- SAT Hospital - Govt Medical College Thiruvananthapuram, Kerala, India
- JK Lone Hospital Jaipur, Rajasthan, India
- Institute of Child Health Kolkata, India
- All India Institute of Medical Sciences (AIIMS) New Delhi, India
Hunter Outcome Survey (HOS)
NCT03292887
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +17 more
- Locations
-
- Shire Lexington, Massachusetts, United States
NCT03920540
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +23 more
- Locations
-
- Samsug Medical Center Seoul, South Korea
NCT03582449
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +17 more
- Locations
-
- Hospital Pediátrico de Sinaloa Culiacán Rosales, México, Mexico
- IMSS UMAE 25 (INSTITUTO MEXICANO DEL SEGURO SOCIAL UNIDAD MEDICA DE ALTA ESPECIALIDAD No 25) Monterrey, Nuevo León, Mexico
- Hospital del Niño Tabasqueño Villahermosa, Tabasco, Mexico
- Hospital Centenario Miguel Hidalgo Aguascalientes, Mexico
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +23 more
- Locations
-
- University of North Carolina at Chapel Hill Chapel Hill, North Carolina, United States
- Birmingham Children's Hospital Birmingham, United Kingdom
- Birmingham Children's Hospital NHS Foundation Trust Birmingham, United Kingdom
NCT00937794
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +17 more
- Locations
-
- University of North Carolina at Chapel Hill Chapel Hill, North Carolina, United States
- Birmingham Children's Hospital Birmingham, United Kingdom
NCT02055118
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +23 more
- Locations
-
- Children's Hospital and Research Center at Oakland Oakland, California, United States
- Ann & Robert H Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- University of North Carolina Chapel Hill, North Carolina, United States
- Women's and Children's Hospital, 72 King William Road North Adelaide, Australia
NCT00630747
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +24 more
- Locations
-
- St. Joseph's Hospital Phoenix, Arizona, United States
- Pediatric Clinical Research Center, Children's Hospital Oakland Oakland, California, United States
- The Children's Hospital Denver, Colorado, United States
- Harbin Clinic Rome, Georgia, United States
NCT01449240
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +17 more
- Locations
-
- Emory University Decatur, Georgia, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- Children's Hospitals and Clinics of Minnesota Minneapolis, Minnesota, United States
- University of North Carolina, Division of Genetics and Metabolism Chapel Hill, North Carolina, United States
NCT00607386
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +24 more
- Locations
-
- Hospital de Clinicas de Porto Alegre, Servico de Genetica Medica Porto Alegre, Rio Grande do Sul, Brazil
- Instytut Pomnik Centrum Zdrowia Dziecka, Klinika Chorob Metaboliczynch, Endokrynologii i Diabetologii Warsaw, Poland
- National Taiwan University Hospital, Dept. of Pediatrics and Medical Genetics Taipei, Taiwan
NCT00882921
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +23 more
- Locations
-
- Children's Hospital & Research Center Oakland Oakland, California, United States
- Children's Hospitals and Clinics of Minnesota, Division of Genetics Minneapolis, Minnesota, United States
- Hospital de Clinicas de Porto Alegre, Servico de Genetica Medica Porto Alegre, Rio Grande do Sul, Brazil
- Birmingham Children's Hospital Birmingham, United Kingdom
NCT01822184
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Cognition Disorders, Cognitive Dysfunction, +25 more
- Locations
-
- Childrens Hospital & Research Center Oakland Oakland, California, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- University of North Carolina Division of Genetics and Metabolism Chapel Hill, North Carolina, United States
- Hospital Universitario Austral Pilar, Buenos Aires, Argentina
NCT01043640
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +52 more
- Locations
-
- Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States
Safety and Efficacy of Hunterase
NCT01645189
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +17 more
- Locations
-
- Samsug Medical Center Seoul, South Korea
MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis
NCT02171104
- Conditions
- Abnormalities, Multiple, Acyl-CoA Oxidase Deficiency, Adrenoleukodystrophy With Cerebral Involvement, +85 more
- Locations
-
- Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States
Extension Study of Idursulfase-IT Along With Elaprase in Children and Adults With Hunter Syndrome and Cognitive Impairment
NCT06031259
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +17 more
- Locations
-
- M.A.G.I.C. Clinic Calgary, Alberta, Canada
- University of British Columbia Vancouver, British Columbia, Canada
- Hospital for Sick Children Toronto, Ontario, Canada
- Hopital Femme Mere Enfant Bron, Auvergne-Rhône-Alpes, France