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Natural History Study of Homocystinuria Caused by Cystathionine Beta-Synthase Deficiency (ACAPPELLA)
NCT02998710
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +13 more
- Locations
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- Travere Investigational Site - Virtual Site Culver City, California, United States
- Travere Investigational Site (Enrolling 1 to <5 Year-olds Only) Aurora, Colorado, United States
- Travere Investigational Site (Enrolling 1 to <5 Year-olds Only) Washington D.C., District of Columbia, United States
- Travere Investigational Site Atlanta, Georgia, United States