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Published and searchable clinical trials
NCT07082725
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
- Locations
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- UCSF Children's Hospital and Research Center at Oakland Oakland, California, United States
- University of Minnesota Medical School Minneapolis, Minnesota, United States
- Mayo Clinic Children's Center - PIN Rochester, Minnesota, United States
- Children's Medical Center Dallas Dallas, Texas, United States
NCT07054515
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +25 more
- Locations
-
- UCSF Children's Hospital and Research Center at Oakland Oakland, California, United States
- University of Minnesota Medical School Minneapolis, Minnesota, United States
- Mayo Clinic Childrens Center - PIN Rochester, Minnesota, United States
- Children's Medical Center Dallas Dallas, Texas, United States
Evaluation of Biochemical Markers and Clinical Investigation of Niemann-Pick Disease, Type C
NCT00344331
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- National Institutes of Health Clinical Center Bethesda, Maryland, United States
Ruxolitinib With De-Intensified HLH-94 for the Treatment of Hemophagocytic Lymphohistiocytosis (HLH)
NCT06160791
- Conditions
- Hemic and Lymphatic Diseases, Hemophagocytic Lymphohistiocytoses, Histiocytosis, +3 more
- Locations
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- University of California, Irvine Irvine, California, United States
- University of California Davis Comprehensive Cancer Center Sacramento, California, United States
- University of California, San Diego San Diego, California, United States
- University of California, San Francisco San Francisco, California, United States
NCT05588167
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- National Institutes of Health Clinical Center Bethesda, Maryland, United States
NCT03990428
- Conditions
- Erdheim-Chester Disease, Hemic and Lymphatic Diseases, Histiocytosis, +3 more
- Locations
-
- Memorial Sloan Kettering Cancer Center New York, United States
NCT07399704
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +23 more
- Locations
-
- Associação Hospitalar de Prot à Infância Dr. Raul Carneiro Água Verde, Curitiba, Brazil
- Hospital de Clinicas de Porto Alegre Porto Alegre, Rio Grande do Sul, Brazil
- Instituto Nacional de Saúde da Mulher, da Criança e do Adolescente Fernandes Figueira Rio de Janeiro, Brazil
Histiocytic Disorder Follow-up Study
NCT05915208
- Conditions
- Erdheim-Chester Disease, Hemic and Lymphatic Diseases, Histiocytic Disorders, Malignant, +16 more
- Locations
-
- University of Alabama at Birmingham Birmingham, Alabama, United States
NCT03117010
- Conditions
- Hemic and Lymphatic Diseases, Hemophagocytic Lymphohistiocytoses, Histiocytosis, +3 more
- Locations
-
- Samsung Medical Center Seoul, South Korea
Ruxolitinib as First Line Treatment in Primary Haemophagocytic Lymphohistiocytosis (R-HLH)
NCT05762640
- Conditions
- Haemophagocytic Lymphohistiocytosis, Hemic and Lymphatic Diseases, Histiocytosis, +3 more
- Locations
-
- Hopital Necker Enfants malades Paris, Île-de-France Region, France
NCT07545473
- Conditions
- Alzheimer Disease, Arterial Occlusive Diseases, Arteriosclerosis, +44 more
- Locations
-
- The Centre for Eye Research Australia Melbourne, Victoria, Australia
NCT07525466
- Conditions
- Extranodal NK T Cell Lymphoma, Hemic and Lymphatic Diseases, Hemophagocytic Lymphohistiocytosis (HLH), +10 more
- Locations
-
- Beijing Tongren Hospital, Capital Medical University Beijing, China
NCT05163288
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Mayo Clinic Rochester, Minnesota, United States
- The Royal Melbourne Hospital Parkville, Victoria, Australia
- First Faculty of Medicine, Charles University Hospital Prague Prague, Czechia
- University of Giessen Giessen, Germany
NCT06339177
- Conditions
- Arthritis, Arthritis, Juvenile, Autoimmune Diseases, +26 more
- Locations
-
- National Institutes of Health Clinical Center Bethesda, Maryland, United States
- University of Pittsburgh Pittsburgh, Pennsylvania, United States
NCT07454343
- Conditions
- Erdheim-Chester Disease, Erdheim-Chester Disease (ECD), Hemic and Lymphatic Diseases, +3 more
- Locations
-
- National Institute of Health Bethesda, Maryland, United States
- Mayo Clinic Rochester, Minnesota, United States
- Memorial Sloan Kettering Cancer Center New York, United States
- Hopital Pitiè-Salpetriere Paris, France
NCT05277272
- Conditions
- Hemic and Lymphatic Diseases, Hemophagocytic Lymphohistiocytoses, Histiocytosis, +3 more
- Locations
-
- Cincinnati Children's Hospital Medical Center Cincinnati, Ohio, United States
NCT05992532
- Conditions
- Acid Sphingomyelinase Deficiency, Blood Protein Disorders, Brain Diseases, +38 more
- Locations
-
- Hospital Universitario de Álava Vitoria-Gasteiz, Alava, Spain
- Hospital Universitario Torrecárdenas Almería, Spain
- Hospital Son Espases Palma de Mallorca, Balearic Islands, Spain
- Hospital Parc Taulí Sabadell, Barcelona, Spain
NCT03333200
- Conditions
- ALD, Alpha-Mannosidosis, Batten Disease, +78 more
- Locations
-
- UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
NCT05093335
- Conditions
- Blood Protein Disorders, Cardiovascular Diseases, Erdheim-Chester Disease, +22 more
- Locations
-
- Memorial Sloan Kettering Cancer Center New York, United States
NCT05898477
- Conditions
- Hemic and Lymphatic Diseases, Hemophagocytic Lymphohistiocytoses, Histiocytosis, +9 more
- Locations
-
- University of Alabama at Birmingham Birmingham, Alabama, United States