Recruiting Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT NCT01962415 Conditions Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +125 more Locations UPMC Children's Hospital of Pittsburgh — Pittsburgh, Pennsylvania, United States View Trial Details
Recruiting Modeling Macrophages Activation Pattern in X-linked Adrenoleukodystrophy, Metachromatic Leukodystrophy and Adult Onset Leukoencephalopathy With Axonal Spheroids and Pigmented Glia NCT04925349 Conditions Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +37 more Locations AP-HP Hôpital Bicêtre — Le Kremlin-Bicêtre, France AP-HP Hôpital La Pitié Salpêtrière — Paris, France View Trial Details
Enrolling by Invitation A Study to Assess CSF1R-related Leukoencephalopathy After Stem Cell Transplantation NCT04503213 Conditions ALSP, Brain Diseases, CSF1R-related Leukoencephalopathy, +6 more Locations Mayo Clinic in Florida — Jacksonville, Florida, United States View Trial Details
Active, Not Recruiting MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis NCT02171104 Conditions Abnormalities, Multiple, Acyl-CoA Oxidase Deficiency, Adrenoleukodystrophy With Cerebral Involvement, +85 more Locations Masonic Cancer Center, University of Minnesota — Minneapolis, Minnesota, United States View Trial Details