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Recruiting
GSD VI and GSD IX Natural History
NCT04454216
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, GLYCOGEN STORAGE DISEASE IXa1, +13 more
- Locations
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- Duke University Durham, North Carolina, United States
Active, Not Recruiting
Early Check: Expanded Screening in Newborns
NCT03655223
- Conditions
- 17 Alpha-Hydroxylase Deficiency, 3-Hydroxy-3-Methylglutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, +456 more
- Locations
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- RTI International Research Triangle Park, North Carolina, United States