Completed Pompe Telemedicine Developmental Study NCT02950298 Conditions Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +14 more Locations Duke University Medical Center — Durham, North Carolina, United States View Trial Details
Active, Not Recruiting Early Check: Expanded Screening in Newborns NCT03655223 Conditions 17 Alpha-Hydroxylase Deficiency, 3-Hydroxy-3-Methylglutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, +456 more Locations RTI International — Research Triangle Park, North Carolina, United States View Trial Details