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NCT00001405
- Conditions
- Chronic Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, +18 more
- Locations
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- National Institutes of Health Clinical Center Bethesda, Maryland, United States
NCT07608432
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DMD, Duchenne Muscular Dystrophy (DMD), +21 more
- Locations
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- Rare Disease Research, LLC Hillsborough, North Carolina, United States
Recruiting
A Phase 3 Study of NTLA-2001 in ATTRv-PN
NCT06672237
- Conditions
- Amyloid Neuropathies, Amyloid Neuropathies, Familial, Amyloidosis, +23 more
- Locations
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- Hospital Británico de Buenos Aires Buenos Aires, Argentina
- Hospital Italiano de Buenos Aires (HIBA) Buenos Aires, Argentina
- Hospital El Cruce San Juan Bautista, Argentina
- Hospital das Clinicas da Universidade Estadual de Campinas (UNICAMP) Campinas, Brazil
NCT05425745
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyslipidemias, Familial Hypercholesterolemia, +14 more
- Locations
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- Site 01022 Jonesboro, Arkansas, United States
- Site 01015 Toluca Lake, California, United States
- Site 01009 Sarasota, Florida, United States
- Site 01023 Boise, Idaho, United States
NCT02916888
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dermatitis, Dermatitis, Atopic, +10 more
- Locations
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- Yale Dermatology Associates New Haven, Connecticut, United States