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NCT02362438
- Conditions
- Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Gene Transfer, +10 more
- Locations
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- National Institutes of Health Clinical Center Bethesda, Maryland, United States
NCT03734588
- Conditions
- Adeno-Associated Virus (AAV), Blood Coagulation Disorder, Blood Coagulation Disorders, +18 more
- Locations
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- Orthopaedic Institute for Children Los Angeles, California, United States
- Illinois Bleeding and Clotting Disorders Institute Peoria, Illinois, United States
- University of Michigan Ann Arbor, Michigan, United States
- Mississippi Center for Advanced Medicine Madison, Mississippi, United States
NCT00427726
- Conditions
- Gene Transfer
- Locations
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- National Institutes of Health Clinical Center, 9000 Rockville Pike Bethesda, Maryland, United States