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A Study of the Efficacy and Safety of Eliglustat Tartrate (Genz-112638) in Type 1 Gaucher Patients
NCT00358150
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
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- New York University New York, United States
- New York, United States
- Aprillus Asistencia e Investigación Buenos Aires, Argentina
- Hospital de Oncologia Maria Curie Buenos Aires, Argentina
NCT00364858
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Children's National Medical Center Washington D.C., District of Columbia, United States
- University Research Foundation for Lysosomal Storage Disease, Inc. Coral Springs, Florida, United States
- Emory University Atlanta, Georgia, United States
- Children's Memorial Hospital Chicago, Illinois, United States
NCT00365131
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Coral Springs, Florida, United States