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Published and searchable clinical trials
NCT06188325
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
- Locations
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- M.D.Covance Clinical Research Unit 1341 W Dallas, Texas, United States
A Study to Evaluate Pharmacokinetic Parameters and Safety of Eliglustat Absorption Through the Mouth
NCT06193304
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
- Locations
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- Covance Clinical Researsh Unit Evansville, Indiana, United States
NCT01586455
- Conditions
- Acute Lymphocytic Leukemia, Acute Myelogenous Leukemia, Adrenal Gland Diseases, +84 more
- Locations
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- Children's Hospital Colorado Denver, Colorado, United States
- New York Medical College Valhalla, New York, United States
- University of Utah Salt Lake City, Utah, United States
Intravenous N-acetylcysteine for the Treatment of Gaucher's Disease and Parkinson's Disease
NCT01427517
- Conditions
- Basal Ganglia Diseases, Brain Diseases, Brain Diseases, Metabolic, +22 more
- Locations
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- University of Minnesota Minneapolis, Minnesota, United States
NCT00176904
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +55 more
- Locations
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- Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States
NCT00001289
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +23 more
- Locations
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- National Institutes of Health Clinical Center, 9000 Rockville Pike Bethesda, Maryland, United States
NCT00001416
- Conditions
- Bone Diseases, Brain Diseases, Brain Diseases, Metabolic, +17 more
- Locations
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- National Institute of Neurological Disorders and Stroke (NINDS) Bethesda, Maryland, United States
Phase II Randomized Study of Alendronate Sodium for Osteopenia in Patients With Gaucher's Disease
NCT00004488
- Conditions
- Bone Diseases, Bone Diseases, Metabolic, Brain Diseases, +23 more
- Locations
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- Children's Hospital Medical Center - Cincinnati Cincinnati, Ohio, United States
- Wright State University School of Medicine Dayton, Ohio, United States
- Shaare Zedek Medical Center Jerusalem, Israel
NCT00001234
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
- Locations
-
- National Institute of Neurological Disorders and Stroke (NINDS) Bethesda, Maryland, United States
NCT00001410
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
- Locations
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- National Institute of Mental Health (NIMH) Bethesda, Maryland, United States
NCT00004294
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
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- University of Pittsburgh Pittsburgh, Pennsylvania, United States