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First-in-human Study of UX016 in GNEM
NCT07511556
- Conditions
- Distal myopathy, Nonaka type, GNE Myopathy
- Locations
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- Clinical Trial Site Orange, California, United States
- Clinical Trial Site Iselin, New Jersey, United States
NCT01417533
- Conditions
- Distal myopathy, Nonaka type, GNE Myopathy, GNE Related Diseases
- Locations
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- National Institutes of Health Clinical Center Bethesda, Maryland, United States
- Conditions
- Distal Myopathy With Rimmed Vacuoles, Distal Myopathy, Nonaka Type, Distal myopathy, Nonaka type, +2 more
- Locations
-
- University of California, Irvine Irvine, California, United States
- Washington University School of Medicine St Louis, Missouri, United States
- New York University School of Medicine New York, United States
- Icahn School of Medicine at Mount Sinai New York, United States
NCT02346461
- Conditions
- Distal myopathy, Nonaka type, GNE Myopathy
- Locations
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- National Institutes of Health Clinical Center, 9000 Rockville Pike Bethesda, Maryland, United States
NCT01784679
- Conditions
- Disease Attributes, Distal Myopathy With Rimmed Vacuoles (DMRV), Distal myopathy, Nonaka type, +7 more
- Locations
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- University of California, Irvine Irvine, California, United States
- Bulgarian Neuromuscular Disease Association Sofia, Bulgaria
- McMaster University Hamilton, Ontario, Canada
- Association Institut de Myologie Paris, France
- Conditions
- Distal myopathy, Nonaka type, GNE Myopathy, Hereditary Inclusion Body Myopathy (hIBM)
- Locations
-
- UCLA Medical Center Los Angeles, California, United States
- Washington University School of Medicine St Louis, Missouri, United States
- NYU Medical Center New York, United States
- Hadassah University Hospital Jerusalem, Israel
NCT01634750
- Conditions
- Distal myopathy, Nonaka type, GNE Myopathy, Hereditary Inclusion Body Myopathy (hIBM)
- Locations
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- National Institutes of Health Clinical Center, 9000 Rockville Pike Bethesda, Maryland, United States
NCT01517880
- Conditions
- Distal myopathy, Nonaka type, GNE Myopathy, Hereditary Inclusion Body Myopathy
- Locations
-
- UCLA Medical Center Los Angeles, California, United States
- Washington University School of Medicine St Louis, Missouri, United States
- New York University School of Medicine New York, United States
- Hadassah University Hospital Jerusalem, Israel
Active, Not Recruiting
Multi-Center Study of ManNAc for GNE Myopathy
NCT04231266
- Conditions
- Distal myopathy, Nonaka type, GNE Myopathy
- Locations
-
- UCLA Los Angeles, California, United States
- University of Iowa Iowa City, Iowa, United States
- University of Kansas, Medical Center Kansas City, Kansas, United States
- NIH Clinical Center Bethesda, Maryland, United States