Recruiting Longitudinal Study of Neurodegenerative Disorders NCT03333200 Conditions ALD, Alpha-Mannosidosis, Batten Disease, +78 more Locations UPMC Children's Hospital of Pittsburgh — Pittsburgh, Pennsylvania, United States View Trial Details
Not Yet Recruiting Prenatal Intravenous Gene Transfer With an AAV9 Vector Expressing Human Beta-galactosidase in Type I and Type II GM1 Gangliosidosis Clinical Trial NCT07479953 Conditions Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +18 more Locations Not specified View Trial Details
