Not Yet Recruiting Treatment Frequency Reduction in Pompe Disease NCT06575829 Conditions Acid Maltase Deficiency, Brain Diseases, Brain Diseases, Metabolic, +15 more Locations Not specified View Trial Details
Active, Not Recruiting Developing a Management Approach for Patients With "Late-Onset" Pompe Disease NCT03694561 Conditions Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more Locations Duke University — Durham, North Carolina, United States View Trial Details