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NCT07615400
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +11 more
- Locations
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- Children's Hospital of Orange County Orange, California, United States
- University of Minnesota Health Minneapolis, Minnesota, United States
- Indira Gandhi Institute of Child Health, Department of Pediatric Neurology Bengaluru, India
- Erasmus University Medical Center Rotterdam, Netherlands
NCT01891422
- Conditions
- Alpha Mannosidosis, Aspartylglucosaminuria, Beta Mannosidosis, +29 more
- Locations
-
- Greenwood Genetic Center North Charleston, South Carolina, United States
NCT01586455
- Conditions
- Acute Lymphocytic Leukemia, Acute Myelogenous Leukemia, Adrenal Gland Diseases, +84 more
- Locations
-
- Children's Hospital Colorado Denver, Colorado, United States
- New York Medical College Valhalla, New York, United States
- University of Utah Salt Lake City, Utah, United States
NCT01043640
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +52 more
- Locations
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- Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States
NCT00176904
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +55 more
- Locations
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- Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States
Completed
Unrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood Cells
NCT00730314
- Conditions
- Agranulocytosis, Albinism, Anemia, +77 more
- Locations
-
- Children Hospital Los Angeles Los Angeles, California, United States
Active, Not Recruiting
MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis
NCT02171104
- Conditions
- Abnormalities, Multiple, Acyl-CoA Oxidase Deficiency, Adrenoleukodystrophy With Cerebral Involvement, +85 more
- Locations
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- Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States