Recruiting Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford NCT01793168 Conditions 1p36 Deletion Syndrome, 3-Methylglutaconic Aciduria, Type V, 4p Deletion Syndrome, Non-Wolf-Hirschhorn Syndrome, +698 more Locations Sanford Health — Sioux Falls, South Dakota, United States Online Patient Enrollment System — Sydney, Australia View Trial Details
Completed Treatment of Fragile-X Associated Tremor/Ataxia Syndrome (FXTAS) With Allopregnanolone NCT02603926 Conditions Fragile X Tremor Ataxia Syndrome, Fragile X-associated Tremor/Ataxia Syndrome Locations UC Davis MIND Institute — Sacramento, California, United States View Trial Details
Completed Memantine Treatment in Fragile X-Associated Tremor/Ataxia Syndrome NCT00584948 Conditions Fragile X Premutation Carriers, Fragile X Tremor Ataxia Syndrome, Fragile X-associated Tremor/Ataxia Syndrome Locations UC Davis MIND Institute — Sacramento, California, United States University of Colorado Health Sciences Center — Aurora, Colorado, United States View Trial Details