Active, Not Recruiting Long-Term Follow-up of Subjects With Fanconi Anaemia Subtype A Treated With ex Vivo Gene Therapy NCT04437771 Conditions Anemia, Anemia, Aplastic, Anemia, Hypoplastic, Congenital, +20 more Locations Hospital Infantil Universitario Niño Jesús (HIUNJ) — Madrid, Spain View Trial Details
Active, Not Recruiting Gene Therapy for Fanconi Anemia, Complementation Group A NCT04248439 Conditions Anemia, Bone Marrow Diseases, Bone Marrow Failure Disorders, +13 more Locations Stanford University — Stanford, California, United States University of Minnesota — Minneapolis, Minnesota, United States View Trial Details