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Recruiting
A Clinical Study to Assess Sutacimig in Participants With Congenital Factor VII Deficiency
NCT07347249
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +7 more
- Locations
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- Royal London Hospital London, United Kingdom
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +10 more
- Locations
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- California Clinical Trials Medical Group (CCTMG) Glendale, California, United States
- Children's Hospital Los Angeles Los Angeles, California, United States
- Rush University Medical Center Chicago, Illinois, United States
- LA Center for Bleeding and Clotting Disorders - Metairie Metairie, Louisiana, United States
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +9 more
- Locations
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- Xiangya Hospital of Central South University Changsha, China
- The First Affiliated Hospital of University of Science and Technology of China Hefei, China
- Jinan Central Hospital Jinan, China
- The First Hospital of Lanzhou University Lanzhou, China
Enrolling by Invitation
Palliative Care Needs of Children With Rare Diseases and Their Families
NCT06938542
- Conditions
- Abnormalities, Multiple, Anxiety Disorders, Arthrogryposis Congenita Multiplex With Intestinal Atresia, +84 more
- Locations
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- Children's National Hospital Washington D.C., District of Columbia, United States
Not Yet Recruiting
A Phase II Exploratory Study of SR604 Injection Evaluating the Safety and Efficacy in the Treatment of Congenital Coagulation Factor VII Deficiency
NCT07711158
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +6 more
- Locations
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- Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences Tianjin, China
NCT05651061
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +8 more
- Locations
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- Anhui Provincial Hospital Hefei, Anhui, China
- Henan Provincial Cancer Hospital Zhengzhou, Henan, China
- Xiangya Hospital, Central South University Changsha, Hunan, China
- Affiliated Hospital of Xuzhou Medical University Xuzhou, Jiangsu, China
NCT03372993
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Blood Platelet Disorders, +11 more
- Locations
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- Iranian Blood Transfusion Organization (IBTO) Tehran, Iran
- MAHTA (Iranian Hemophilia and Thrombophilia Association) Tehran, Iran
NCT03079063
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +6 more
- Locations
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- Hemophilia Center - Hematology & Oncology Dept. Shiraz University of Medical Science Shiraz, Iran
- Comprehensive Hemophilia Care Center Tehran, Iran
NCT01269138
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +6 more
- Locations
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- San Salvatore Hospital L’Aquila, AQ, Italy
Active, Not Recruiting
Early Check: Expanded Screening in Newborns
NCT03655223
- Conditions
- 17 Alpha-Hydroxylase Deficiency, 3-Hydroxy-3-Methylglutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, +456 more
- Locations
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- RTI International Research Triangle Park, North Carolina, United States