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Showing 1–16 of 16 trials
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Published and searchable clinical trials
NCT07038200
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, FSH Muscular Dystrophy, FSHD, +25 more
- Locations
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- University of California Irvine Orange, California, United States
- Stanford University Palo Alto, California, United States
- University of Colorado Denver, Colorado, United States
- University of Florida Gainesville, Florida, United States
NCT07409142
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, FSH, FSH Muscular Dystrophy, +17 more
- Locations
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- FSHD Society Randolph, Massachusetts, United States
NCT05019625
- Conditions
- Becker Muscular Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, +15 more
- Locations
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- Boston Children's Hospital Boston, Massachusetts, United States
- Brigham and Women's Hospital Boston, Massachusetts, United States
- Massachusetts General Hospital Boston, Massachusetts, United States
- Wake Forest University Winston-Salem, North Carolina, United States
NCT00082108
- Conditions
- Congenital Myotonic Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Facioscapulohumeral Muscular Dystrophy, +18 more
- Locations
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- University of Rochester Medical Center, Department of Neurology Rochester, New York, United States
NCT01931644
- Conditions
- ADD/ADHD, Abnormalities, Multiple, Acquired Immunodeficiency Syndrome, +282 more
- Locations
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- Sanguine Biosciences Los Angeles, California, United States
NCT02836418
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Facioscapulohumeral Muscular Dystrophy, Genetic Diseases, Inborn, +9 more
- Locations
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- University of California, Irvine, ALS and Neuromuscular Center Irvine, California, United States
- Stanford University Stanford, California, United States
- University of Utah Salt Lake City, Utah, United States
- Rigshospitalet, University of Copenhagen Copenhagen, Denmark
NCT02579239
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Facioscapulohumeral Muscular Dystrophy, Genetic Diseases, Inborn, +10 more
- Locations
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- University of California, Irvine, ALS and Neuromuscular Center Irvine, California, United States
- Kennedy Krieger Institute; The Johns Hopkins University School of Medicine Baltimore, Maryland, United States
- OSU Wexner Medical Center Columbus, Ohio, United States
- Rigshospitalet, University of Copenhagen Copenhagen, Denmark
NCT02531217
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Facioscapulohumeral Muscular Dystrophy, Genetic Diseases, Inborn, +7 more
- Locations
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- aTyr Pharma Investigative Site Columbus, Ohio, United States
- aTyr Pharma Investigative Site Rome, Italy
- aTyr Pharma Investigative Site Nijmegen, Netherlands
Study of Testosterone and rHGH in FSHD
NCT03123913
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Facioscapulohumeral Muscular Dystrophy, Genetic Diseases, Inborn, +7 more
- Locations
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- University of Rochester Rochester, New York, United States
NCT02413190
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Facioscapulohumeral Muscular Dystrophy, Genetic Diseases, Inborn, +7 more
- Locations
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- Kennedy Krieger Institute, Johns Hopkins School of Medicine Baltimore, Maryland, United States
- Concord Hospital Neurology Department, Hospital Road, Concord NSW 2139 Sydney, Australia
NCT02766985
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Facioscapulohumeral Muscular Dystrophy, Genetic Diseases, Inborn, +7 more
- Locations
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- University of Kansas Medical Center Kansas City, Kansas, United States
- University of Utah Salt Lake City, Utah, United States
NCT01437345
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Facioscapulohumeral Muscular Dystrophy, Genetic Diseases, Inborn, +7 more
- Locations
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- University of California - Davis Sacramento, California, United States
- Children's National Medical Center Washington D.C., District of Columbia, United States
- University of Minnesota Minneapolis, Minnesota, United States
- Washington University St Louis, Missouri, United States
NCT00104078
- Conditions
- Becker Muscular Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Facioscapulohumeral Muscular Dystrophy, +12 more
- Locations
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- Washington D.C., District of Columbia, United States
- Kansas City, Kansas, United States
- Baltimore, Maryland, United States
- Boston, Massachusetts, United States
A First-in-human Study of EPI-321 in Facioscapulohumeral Muscular Dystrophy
NCT06907875
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Facioscapulohumeral Muscular Dystrophy, Genetic Diseases, Inborn, +7 more
- Locations
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- David Geffen School of Medicine at University of California, Los Angeles Los Angeles, California, United States
- Rare Disease Research Atlanta, Georgia, United States
- Kennedy Krieger Institute, Center for Genetic Muscle Disorders Baltimore, Maryland, United States
- University of Massachusetts Chan Medical School Worcester, Massachusetts, United States
Clinical Trial Readiness to Solve Barriers to Drug Development in FSHD
NCT03458832
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Facioscapulohumeral Muscular Dystrophy, Genetic Diseases, Inborn, +7 more
- Locations
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- University of California Los Angeles Los Angeles, California, United States
- University of Kansas Medical Center Kansas City, Kansas, United States
- Kennedy Krieger Institute Baltimore, Maryland, United States
- University of Rochester Medical Center Rochester, New York, United States
Magnetic Resonance Imaging and Spectroscopy Biomarkers for Facioscapulohumeral Muscular Dystrophy
NCT01671865
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Facioscapulohumeral Muscular Dystrophy, Genetic Diseases, Inborn, +7 more
- Locations
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- Doris Leung Baltimore, Maryland, United States