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Enrolling by Invitation
Phase 1/2 Study of FRF-001, an AAV-9 Gene Therapy, in Patients With FOXG1 Syndrome (FS)
NCT07293546
- Conditions
- FOXG1 Syndrome
- Locations
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- Texas Children's Hospital (Baylor College of Medicine) Houston, Texas, United States
Enrolling by Invitation
Palliative Care Needs of Children With Rare Diseases and Their Families
NCT06938542
- Conditions
- Abnormalities, Multiple, Anxiety Disorders, Arthrogryposis Congenita Multiplex With Intestinal Atresia, +84 more
- Locations
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- Children's National Hospital Washington D.C., District of Columbia, United States
NCT02738281
- Conditions
- CDKL5 Disorder, CDKL5 deficiency disorder, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +11 more
- Locations
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- University of Alabama at Birmingham Birmingham, Alabama, United States
- UCSF Oakland Benioff Children's Hospital Oakland, California, United States
- University of California San Diego San Diego, California, United States
- University of Colorado Denver Denver, Colorado, United States