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Recruiting
Study to Evaluate Sepofarsen in Subjects With Leber Congenital Amaurosis (LCA) Type 10 (HYPERION)
NCT06891443
- Conditions
- Blindness, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +28 more
- Locations
-
- UCSF Wayne and Gladys Valley Center for Vision San Francisco, California, United States
- University of Miami - Bascom Palmer Eye Institute Miami, Florida, United States
- University of Iowa Iowa City, Iowa, United States
- University of Minnesota Medical School Minneapolis, Minnesota, United States
NCT03396042
- Conditions
- Blindness, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +17 more
- Locations
-
- Bascom Palmer Eye Institute Miami, Florida, United States
- Massachusetts Eye and Ear Infirmary Boston, Massachusetts, United States
- W.K. Kellogg Eye Center Ann Arbor, Michigan, United States
- Casey Eye Institute - OHSU Portland, Oregon, United States
NCT03780257
- Conditions
- Abnormalities, Multiple, Blindness, Congenital Abnormalities, +27 more
- Locations
-
- Center for Clinical Research Operations, Massachusetts Eye and Ear Boston, Massachusetts, United States
- University of Michigan, Kellogg Eye Center Ann Arbor, Michigan, United States
- Casey Eye Institute, Oregon Health & Science University Portland, Oregon, United States
- Retina Foundation of the Southwest Dallas, Texas, United States
Active, Not Recruiting
Study to Evaluate Ultevursen in Subjects With Retinitis Pigmentosa (RP) Due to Mutations in Exon 13 of the USH2A Gene
NCT06627179
- Conditions
- Abnormalities, Multiple, Blindness, Congenital Abnormalities, +28 more
- Locations
-
- The University of California, San Francisco San Francisco, California, United States
- Bascom Palmer Eye Institute/University of Miami Miami, Florida, United States
- Emory University Atlanta, Georgia, United States
- Massachusetts Eye and Ear Boston, Massachusetts, United States
Active, Not Recruiting
A Study to Evaluate Efficacy, Safety, Tolerability and Exposure After a Repeat-dose of Sepofarsen (QR-110) in LCA10 (ILLUMINATE)
NCT03913143
- Conditions
- Blindness, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +26 more
- Locations
-
- University of Iowa Iowa City, Iowa, United States
- Universitair Ziekenhuis Gent (UZ) Ghent, Belgium
- INRET Clínica/ Santa Casa de Misericórdia de Belo Horizonte Belo Horizonte, Minas Gerais, Brazil
- Federal University of São Paulo - Hospital São Paulo (UNIFESP-HSP) São Paulo, Brazil