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Showing 1–16 of 16 trials
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Published and searchable clinical trials
HELIOS: Open-Label, Long-Term Extension Study to Investigate the Safety, Tolerability, and Efficacy of DISC-1459 (Bitopertin) in Participants With EPP or XLP
NCT05883748
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Erythropoietic Protoporphyria, +10 more
- Locations
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- University of Alabama Hospital Birmingham, Alabama, United States
- University of California San Francisco San Francisco, California, United States
- University of Miami Miller School of Medicine Miami, Florida, United States
- Massachusetts General Hospital Boston, Massachusetts, United States
NCT06388642
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Erythropoietic Protoporphyria, +10 more
- Locations
-
- CLINUVEL Site Leuven, Belgium
- CLINUVEL Site Rotterdam, Netherlands
NCT05020184
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Erythropoietic Protoporphyria, +13 more
- Locations
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- Massachusetts General Hospital Boston, Massachusetts, United States
- Atrium Health Wake Forest Baptist Medical Center Winston-Salem, North Carolina, United States
- University of Texas Medical Branch Galveston, Texas, United States
NCT05308472
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Erythropoietic Protoporphyria, +10 more
- Locations
-
- University of Alabama Hospital Birmingham, Alabama, United States
- University of California San Francisco San Francisco, California, United States
- University of Miami Miller School of Medicine Miami, Florida, United States
- Massachusetts General Hospital Boston, Massachusetts, United States
NCT05572125
- Conditions
- Anemia, Anemia, Hypochromic, Anemia, Iron-Deficiency, +18 more
- Locations
-
- Bispebjerg Hospital Copenhagen, Denmark
NCT00979745
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Erythropoietic Protoporphyria, +10 more
- Locations
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- HUS:n Iho-ja allergiasairaala (Skin and Allergy Hospital) Helsinki, Finland
- Centre Français des Porphyries, Hôpital Louis Mourier Colombes, Cedex, France
- Department of Dermatology , Heinrich-Heine-University Duesseldorf Düsseldorf, Germany
- Beaumont Hospital, Department of Dermatology Dublin, Ireland
NCT04578496
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Erythropoietic Protoporphyria, +10 more
- Locations
-
Not specified
NCT02979249
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, EPP, +14 more
- Locations
-
- University of Alabama, Birmingham Birmingham, Alabama, United States
- University of California San Francisco, California, United States
- Icahn School of Medicine at Mount Sinai New York, United States
- Wake Forest University Health Sciences Winston-Salem, North Carolina, United States
NCT01688895
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, EPP, +18 more
- Locations
-
- University of Alabama, Birmingham Birmingham, Alabama, United States
- University of California, San Francisco San Francisco, California, United States
- Icahn School of Medicine at Mount Sinai New York, United States
- Wake Forest University Health Sciences Winston-Salem, North Carolina, United States
NCT01097044
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Erythropoietic Protoporphyria, +10 more
- Locations
-
- University of Alabama Birmingham, Alabama, United States
- University of California, San Francisco San Francisco, California, United States
- Mt. Sinai New York, United States
- Carolina's Medical Center Cannon Research Charlotte, North Carolina, United States
NCT04053270
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Erythropoietic Protoporphyria, +10 more
- Locations
-
Not specified
NCT01605136
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Erythropoietic Protoporphyria, +10 more
- Locations
-
- University of Alabama Birmingham, Alabama, United States
- University of California, San Francisco San Francisco, California, United States
- Henry Ford Medical Center Detroit, Michigan, United States
- Mt. Sinai New York, United States
NCT03682731
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Erythropoietic Protoporphyria, +10 more
- Locations
-
- Bispebjerg Hospital Copenhagen, Denmark
- Bispebjerg Hospital Copenhagen NV, Denmark
NCT01422915
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Erythropoietic Protoporphyria, +10 more
- Locations
-
- Brigham & Women's Hospital Boston, Massachusetts, United States
NCT00004940
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Disease Attributes, +15 more
- Locations
-
Not specified
NCT00004831
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Disease Attributes, +15 more
- Locations
-
Not specified