Completed Study of AOC 1001 in Adult Myotonic Dystrophy Type 1 (DM1) Patients NCT05027269 Conditions Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Dystrophy Myotonic, +15 more Locations University of California Los Angeles — Los Angeles, California, United States Stanford University — Palo Alto, California, United States University of Colorado — Denver, Colorado, United States University of Florida — Gainesville, Florida, United States View more locations Show fewer locations Loading locations... View Trial Details
Active, Not Recruiting Global Study of Del-desiran for the Treatment of DM1 NCT06411288 Conditions Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Dystrophy Myotonic, +21 more Locations Stanford University — Stanford, California, United States University of Colorado — Denver, Colorado, United States University of Florida — Gainesville, Florida, United States University Research Center of South Florida — Tampa, Florida, United States View all 34 locations View more locations Show fewer locations Loading locations... View Trial Details