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Published and searchable clinical trials
NCT07674758
- Conditions
- Becker Muscular Dystrophy, Cardiomyopathies, Cardiomyopathy, +14 more
- Locations
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- UC Davis Sacramento, California, United States
- Children's National Washington D.C., District of Columbia, United States
- Lurie Children's Chicago, Illinois, United States
- Riley Children's Hospital Indianapolis, Indiana, United States
NCT07172971
- Conditions
- Cardiomyopathies, Cardiovascular Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +12 more
- Locations
-
- Vanderbilt University Medical Center Nashville, Tennessee, United States
NCT07423026
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy (DMD), Genetic Diseases, Inborn, +8 more
- Locations
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- Oxford University Oxford, United Kingdom
Duchenne Electronic Health Record Study
NCT07609394
- Conditions
- Becker Muscular Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy (DMD), +11 more
- Locations
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- Arkansas Children's Hospital Little Rock, Arkansas, United States
- UC Davis Health Sacramento, California, United States
- Children's Hospital Colorado Aurora, Colorado, United States
- Yale Children's Hospital New Haven, Connecticut, United States
NCT07608432
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DMD, Duchenne Muscular Dystrophy (DMD), +21 more
- Locations
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- Rare Disease Research, LLC Hillsborough, North Carolina, United States
NCT07039799
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy (DMD), Genetic Diseases, Inborn, +9 more
- Locations
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- İstanbul Üniversitesi Cerrahpaşa Tıp Fakültesi Istanbul, Fatih, Turkey (Türkiye)
NCT07038824
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy (DMD), Genetic Diseases, Inborn, +8 more
- Locations
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- University Hospital Gent Ghent, Belgium
- UZ Leuven Leuven, Belgium
- Centre Hospitalier Régional de la Citadelle Liège, Belgium
- IRCCS Ospedale San Raffaele Milan, Italy
Safety and Dystrophin Expression of SPOT-03 in Duchenne Muscular Dystrophy (DMD) Patients
NCT07188012
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy (DMD), Genetic Diseases, Inborn, +8 more
- Locations
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- Shanghai Children's Medical Center Shanghai, Shanghai Municipality, China
NCT07092540
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy (DMD), Genetic Diseases, Inborn, +8 more
- Locations
-
- University of Rochester Rochester, New York, United States
Invasive Home Ventilation in Denmark
NCT07467187
- Conditions
- ALS (Amyotrophic Lateral Sclerosis), Amyotrophic Lateral Sclerosis, Autonomic Nervous System Diseases, +38 more
- Locations
-
- Respiratory Center East Copenhagen, Denmark
NCT06839469
- Conditions
- Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy (DMD), +16 more
- Locations
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- Stanford University Palo Alto, California, United States
- Boston Children's Hospital Boston, Massachusetts, United States
- Columbia University Irving Medical Center New York, United States
Urinary Titin Biomarker in DMD
NCT07332013
- Conditions
- Becker's Muscular Dystrophy (BMD), Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy (DMD), +9 more
- Locations
-
- Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
NCT07515235
- Conditions
- Becker Muscular Dystrophy, Cardiomyopathies, Cardiomyopathy, +13 more
- Locations
-
- AHEPA University Hospital of Thessaloniki Thessaloniki, Greece
NCT07037862
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy (DMD), Genetic Diseases, Inborn, +8 more
- Locations
-
- University Hospital Gent Ghent, Belgium
- UZ Leuven Leuven, Belgium
- Centre Hospitalier Régional de la Citadelle Liège, Belgium
- IRCCS Ospedale San Raffaele Milan, Italy
NCT07286565
- Conditions
- Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy (DMD), +14 more
- Locations
-
- Centre de référence des maladies neuromusculaire, Centre Hospitalier Régional de la Citadelle Liège, Belgium
Fear of Falling in Muscular Dystrophy
NCT07129954
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy (DMD), Fear of Falling, +10 more
- Locations
-
- Azienda Ospedaliera Universitaria Integrata Verona - UOC di Neuroriabilitazione Verona, verona, Italy
NCT06925269
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy (DMD), Genetic Diseases, Inborn, +8 more
- Locations
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- Red Nucleus Yardley, Pennsylvania, United States
NCT06900049
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy (DMD), Genetic Diseases, Inborn, +8 more
- Locations
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- Shanghai Children's Medical Center, Shanghai Jiao Tong University School of Medicine Shanghai, Shanghai Municipality, China
Evaluation of the Safety and Efficacy of BBM-D101 to Treat Patients with Duchenne Muscular Dystrophy
NCT06641895
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy (DMD), Genetic Diseases, Inborn, +8 more
- Locations
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- Shanghai Children's Medical Center Affiliated to Shanghai Jiao Tong University School of Medicine Shanghai, Shanghai Municipality, China
NCT06773988
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy (DMD), Genetic Diseases, Inborn, +8 more
- Locations
-
- Universitaire Ziekenhuizen KU Leuven Leuven, Vlaams-Brabant, Belgium