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Published and searchable clinical trials
NCT06817382
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
-
- USA012 Little Rock, Arkansas, United States
- USA010 Davis, California, United States
- USA009 Los Angeles, California, United States
- USA002 Palo Alto, California, United States
NCT05933057
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
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- Universitaire Ziekenhuizen Leuven Leuven, Belgium
- British Columbia Children's Hospital Vancouver, British Columbia, Canada
- The University of Western Ontario - Children's Health Research Institute London, Ontario, Canada
- University of Ottawa - Children's Hospital of Eastern Ontario Ottawa, Ontario, Canada
NCT07287189
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DMD, Duchenne, +10 more
- Locations
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- University of California Los Angeles Los Angeles, California, United States
- Colorado Children's Aurora, Colorado, United States
- Lurie Children's Chicago, Illinois, United States
- UMass Memorial Medical Center Worcester, Massachusetts, United States
NCT06564974
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
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- Phoenix Children's Hospital Phoenix, Arizona, United States
- Arkansas Childrens Hospital Little Rock, Arkansas, United States
- Loma Linda University Pediatric Subspecialty Clinics Loma Linda, California, United States
- Children's Hospital Los Angeles Los Angeles, California, United States
A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)
NCT07160634
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
-
- Arkansas Children's Hospital Little Rock, Arkansas, United States
- Neurology Rare Disease Center Flower Mound, Texas, United States
- Children's Hospital of the King's Daughters Norfolk, Virginia, United States
- The Children's Hospital of Westmead Sydney, New South Wales, Australia
NCT06138639
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
-
- Arkansas Children's Hospital Little Rock, Arkansas, United States
- University of California, Los Angeles Medical Center Los Angeles, California, United States
- University of California, Davis Sacramento, California, United States
- University of California San Diego, California, United States
NCT07673809
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
-
- Republican Scientific and Practical Center Mother and Child Minsk, Belarus
- Russian Children's Clinical Hospital Moscow, Russia
- National Medical Research Center for Children Moscow, Russia
- Veltischev Research and Clinical Institute for Pediatrics and Pediatric Surgery of the Pirogov Russian National Research Medical University Moscow, Russia
NCT04626674
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
-
- Arkansas Children's Hospital Little Rock, Arkansas, United States
- Stanford University Palo Alto, California, United States
- University of California, Davis Sacramento, California, United States
- Washington University in St. Louis St Louis, Missouri, United States
NCT06124196
- Conditions
- Cardiomyopathies, Cardiovascular Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +16 more
- Locations
-
- Vanderbilt University Medical Center Nashville, Tennessee, United States
NCT06290713
- Conditions
- Aneurysm, Bacterial Infections, Bacterial Infections and Mycoses, +32 more
- Locations
-
- University of Florida Clinical and Translational Research Building Gainesville, Florida, United States
The Duchenne Registry
NCT02069756
- Conditions
- Becker Muscular Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, +12 more
- Locations
-
- The Duchenne Registry / PPMD Washington D.C., District of Columbia, United States
NCT05996003
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DMD, Duchenne Muscular Dystrophy, +10 more
- Locations
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- Children's Hospital Colorado Aurora, Colorado, United States
- Rare Disease Research, LLC - FL Kissimmee, Florida, United States
- Rare Disease Research Atlanta, Georgia, United States
- Ann and Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
Trial of Cell Based Therapy for DMD
NCT06692426
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
-
- Masonic Cancer Center Minneapolis, Minnesota, United States
NCT03882827
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
-
- Centre Hospitalier Universitaire Brugmann Brussels, Belgium
- UZ Leuven Leuven, Belgium
- CHR Hôpital de la Citadelle Liège, Belgium
- University Hospital of Bordeaux Bordeaux, France
NCT06402942
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Gamification, +10 more
- Locations
-
- Lokman Hekim University Ankara, Turkey (Türkiye)
NCT03373968
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
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- University of California - Davis Medical Center - Devis Physical Medicine & Rehabilitation Sacramento, California, United States
- Rady Children's Hospital center - UCSD Department of Neuroscience San Diego, California, United States
- Connecticut Children's Medical Center, Neurology Division Hartford, Connecticut, United States
- Child Health Research Institute Gainesville, Florida, United States
NCT04906460
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
-
- Arkansas Children's Hospital Little Rock, Arkansas, United States
- Rare Disease Research LLC Atlanta, Georgia, United States
- Istiklal Hospital/ Clinical Research Unit Amman, Jordan
- The Specialty Hospital (TSH)/ Advanced Clinical Center Amman, Jordan
NCT05016908
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
-
- Boston Children's Hospital Boston, Massachusetts, United States
- Massachusetts General Hospital Boston, Massachusetts, United States
NCT05019625
- Conditions
- Becker Muscular Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, +15 more
- Locations
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- Boston Children's Hospital Boston, Massachusetts, United States
- Brigham and Women's Hospital Boston, Massachusetts, United States
- Massachusetts General Hospital Boston, Massachusetts, United States
- Wake Forest University Winston-Salem, North Carolina, United States
NCT06093100
- Conditions
- Cardiomyopathies, Cardiovascular Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +16 more
- Locations
-
- Vanderbilt University Medical Center Nashville, Tennessee, United States