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Personalized Antisense Oligonucleotide for A Single Participant With ATN1 Gene Mutation
NCT07084311
- Conditions
- Brain Diseases, Central Nervous System Diseases, Dentatorubral-Pallidoluysian Atrophy, +6 more
- Locations
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- Hawaii Pacific Neuroscience Honolulu, Hawaii, United States
Active, Not Recruiting
Personalized Antisense Oligonucleotide Therapy for A Single Participant With ATN1 Gene Mutation
NCT06706388
- Conditions
- Brain Diseases, Central Nervous System Diseases, Dentatorubral-Pallidoluysian Atrophy, +6 more
- Locations
-
- Columbia University New York, United States
Active, Not Recruiting
Personalized Antisense Oligonucleotide for A Single Participant (nL62541) With ATN1 Gene Mutation
NCT07221760
- Conditions
- Brain Diseases, Central Nervous System Diseases, Dentatorubral-Pallidoluysian Atrophy, +6 more
- Locations
-
- Dell Children's Austin, Texas, United States