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Recruiting
Danon Disease Natural History Study
NCT06214507
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Cardiomyopathies, Cardiovascular Diseases, +15 more
- Locations
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- Phoenix Children's Hospital Phoenix, Arizona, United States
- University of California, San Diego La Jolla, California, United States
- Children's Hospital Colorado Aurora, Colorado, United States
- University of Florida College of Medicine Gainesville, Florida, United States
NCT06092034
- Conditions
- Aortic Stenosis, Subvalvular, Aortic Valve Disease, Aortic Valve Stenosis, +26 more
- Locations
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- University of California, San Diego La Jolla, California, United States
- Boston Children's Hospital Boston, Massachusetts, United States
- Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
- German Heart Center Munich Munich, Germany
NCT07336394
- Conditions
- Amyloid Neuropathies, Amyloid Neuropathies, Familial, Amyloidosis, +53 more
- Locations
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- Fuwai Hospital Beijing, China
NCT06795152
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Cardiomyopathies, Cardiovascular Diseases, +37 more
- Locations
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- Duke University Durham, North Carolina, United States
Completed
Natural History of Danon Disease
NCT05548855
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Cardiomyopathies, Cardiovascular Diseases, +15 more
- Locations
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- Institut klinické a experimentální medicíny (IKEM)- Institute for Clinical and Experimental Medicine Prague, Czechia
- CHU de Nantes, Hôpital Laennec Nantes, France
- APHP, Hôpital de la Pitié Salppêtrière - Charles Foix Paris, France
- CHU de Rennes, Hôpital Pontchaïllou Rennes, France