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NCT07287189
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DMD, Duchenne, +10 more
- Locations
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- University of California Los Angeles Los Angeles, California, United States
- Colorado Children's Aurora, Colorado, United States
- Lurie Children's Chicago, Illinois, United States
- UMass Memorial Medical Center Worcester, Massachusetts, United States
NCT07608432
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DMD, Duchenne Muscular Dystrophy (DMD), +21 more
- Locations
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- Rare Disease Research, LLC Hillsborough, North Carolina, United States
NCT06290713
- Conditions
- Aneurysm, Bacterial Infections, Bacterial Infections and Mycoses, +32 more
- Locations
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- University of Florida Clinical and Translational Research Building Gainesville, Florida, United States
NCT05996003
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DMD, Duchenne Muscular Dystrophy, +10 more
- Locations
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- Children's Hospital Colorado Aurora, Colorado, United States
- Rare Disease Research, LLC - FL Kissimmee, Florida, United States
- Rare Disease Research Atlanta, Georgia, United States
- Ann and Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
NCT01890616
- Conditions
- Constipation, DMD, Pathological Conditions, Signs and Symptoms, +2 more
- Locations
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- Cincinnati Children's Hospital Medical Center Cincinnati, Ohio, United States
Active, Not Recruiting
Ph2 Open-label Study of AOC 1044 in Duchenne Muscular Dystrophy Participants With Mutations Amenable to Exon44 Skipping
NCT06244082
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DMD, Duchenne, +11 more
- Locations
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- Arkansas Children's Hospital Little Rock, Arkansas, United States
- University of California, San Diego, Rady's Children's Hospital La Jolla, California, United States
- UC Davis Medical Center Sacramento, California, United States
- Lucille Packard Children's Hospital at Stanford San Carlos, California, United States