Clinical trial discovery
Find Clinical Trials
Search studies by condition, treatment, location, eligibility, or trial identifier.
Showing 1–10 of 10 trials
Active filters
Clinical trials found
Published and searchable clinical trials
NCT07486934
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +18 more
- Locations
-
- UCSD - Altman Clinical and Translational Research Institute La Jolla, California, United States
- Rare Disease Research, LLC Atlanta, Georgia, United States
- IU Health Neuroscience Center Indianapolis, Indiana, United States
- Roy Blunt NextGen Precision Health Institute Columbia, Missouri, United States
Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Extension
NCT07700225
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +20 more
- Locations
-
- Virginia Commonwealth University Richmond, Virginia, United States
NCT03981575
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +11 more
- Locations
-
- University of California, San Diego La Jolla, California, United States
- University of California, Los Angeles Los Angeles, California, United States
- University of Colorado - Denver Denver, Colorado, United States
- University of Florida Gainesville, Florida, United States
NCT07505342
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +11 more
- Locations
-
- University of Rochester Rochester, New York, United States
NCT07385443
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +14 more
- Locations
-
- Hospitals within the DM1 network Multiple Locations, Andalusia, Spain
- Hospitals within the DM1 network Multiple Locations, Basque Country, Spain
- Hospitals within the DM1 network Multiple Locations, Canary Islands, Spain
- Hospitals within the DM1 network Multiple Locations, Cantabria, Spain
Global Open-Label Extension Study of Del-desiran for the Treatment of DM1
NCT07008469
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +19 more
- Locations
-
- University of California, Los Angeles (UCLA) Los Angeles, California, United States
- Stanford University Stanford, California, United States
- University of Colorado Denver, Colorado, United States
- University of Florida Gainesville, Florida, United States
NCT05027269
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Dystrophy Myotonic, +15 more
- Locations
-
- University of California Los Angeles Los Angeles, California, United States
- Stanford University Palo Alto, California, United States
- University of Colorado Denver, Colorado, United States
- University of Florida Gainesville, Florida, United States
Extension of AOC 1001-CS1 (MARINA) Study in Adult Myotonic Dystrophy Type 1 (DM1) Patients
NCT05479981
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +11 more
- Locations
-
- University of California Los Angeles Los Angeles, California, United States
- Stanford University Palo Alto, California, United States
- University of Colorado Denver, Colorado, United States
- University of Florida Gainesville, Florida, United States
NCT02084407
- Conditions
- Cardiovascular Diseases, DM1, Heart Diseases
- Locations
-
- Institute of Myology Paris, France
Global Study of Del-desiran for the Treatment of DM1
NCT06411288
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Dystrophy Myotonic, +21 more
- Locations
-
- Stanford University Stanford, California, United States
- University of Colorado Denver, Colorado, United States
- University of Florida Gainesville, Florida, United States
- University Research Center of South Florida Tampa, Florida, United States