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NCT05484570
- Conditions
- Abnormalities, Multiple, Bone Diseases, Bone Diseases, Developmental, +24 more
- Locations
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- University of Minnesota- Twin Cities Minneapolis, Minnesota, United States
Recruiting
The Myelin Disorders Biorepository Project
NCT03047369
- Conditions
- 4H Syndrome, ADLD, AGS, +173 more
- Locations
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- Children's Hospital of Los Angeles Los Angeles, California, United States
- Children's Hospital of Orange County Orange, California, United States
- Stanford University (Lucile Packard Children's Hospital) Palo Alto, California, United States
- University of California, Davis (UC Davis Health) Sacramento, California, United States
Recruiting
Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
NCT01793168
- Conditions
- 1p36 Deletion Syndrome, 3-Methylglutaconic Aciduria, Type V, 4p Deletion Syndrome, Non-Wolf-Hirschhorn Syndrome, +698 more
- Locations
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- Sanford Health Sioux Falls, South Dakota, United States
- Online Patient Enrollment System Sydney, Australia
Enrolling by Invitation
Palliative Care Needs of Children With Rare Diseases and Their Families
NCT06938542
- Conditions
- Abnormalities, Multiple, Anxiety Disorders, Arthrogryposis Congenita Multiplex With Intestinal Atresia, +84 more
- Locations
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- Children's National Hospital Washington D.C., District of Columbia, United States
NCT00001813
- Conditions
- Abnormalities, Multiple, Bone Diseases, Bone Diseases, Developmental, +25 more
- Locations
-
- National Institutes of Health Clinical Center Bethesda, Maryland, United States
NCT02699190
- Conditions
- 4H Syndrome, ADLD, AGS, +173 more
- Locations
-
- The Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
NCT01142154
- Conditions
- Abnormalities, Multiple, Bone Diseases, Bone Diseases, Developmental, +13 more
- Locations
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- Children's Hospital Boston Boston, Massachusetts, United States