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Conditions
3-Hydroxy 3-Methyl Glutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, 3-Hydroxy-3-Methylglutaryl-CoA Synthase 2 Deficiency, +368 more
Locations
  • CRMN, Hôpital La Citadelle Liège, Wallonia, Belgium

NCT04612764

Conditions
ARGI Deficiency, ASL Deficiency, ASS Deficiency, +22 more
Locations
  • Children's Hospital Colorado Aurora, Colorado, United States
  • Children's National Medical Center Washington D.C., District of Columbia, United States
  • The Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
  • Baylor College of Medicine Houston, Texas, United States