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NCT05819866
- Conditions
- Cerebral Adrenoleukodystrophy (cALD)
- Locations
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- Stanford University Medical Center Palo Alto, California, United States
- Neuro Medicine Hospital / UF Health Gainesville, Florida, United States
- Kennedy Krieger Institute Baltimore, Maryland, United States
- Massachusetts General Hospital Boston, Massachusetts, United States
NCT06224413
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +22 more
- Locations
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- Boston Children's Hospital Boston, Massachusetts, United States
- Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
- UT Southwestern Medical Center Dallas, Texas, United States
NCT03852498
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +22 more
- Locations
-
- Lucile Packard Children's Hospital Palo Alto, California, United States
- Boston Children's Hospital/Massachusetts General Hospital Boston, Massachusetts, United States
- University of Minnesota Minneapolis, Minnesota, United States
- Hôpital Robert Debré Paris, France
NCT01896102
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +22 more
- Locations
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- Mattel Children's Hospital UCLA/Ronald Reagan UCLA Medical Center Los Angeles, California, United States
- Boston Children's Hospital/Massachusetts General Hospital Boston, Massachusetts, United States
- University of Minnesota Minneapolis, Minnesota, United States
- Medeos SRL Buenos Aires, Argentina
Active, Not Recruiting
Long-term Follow-up of Participants With Cerebral Adrenoleukodystrophy Who Were Treated With Lenti-D Drug Product
NCT02698579
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +24 more
- Locations
-
- Mattel Children's Hospital-UCLA Los Angeles, California, United States
- Lucile Packard Children's Hospital - Stanford Palo Alto, California, United States
- Boston Children's Hospital/Massachusetts General Hospital Boston, Massachusetts, United States
- University of Minnesota Minneapolis, Minnesota, United States