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NCT02214160
- Conditions
- Carnitine Palmitoyltransferase (CPT I or CPT II) Deficiency, Carnitine-acylcarnitine Translocase (CACT) Deficiency, Long-chain 3-hydroxy-acyl-CoA Dehydrogenase (LCHAD) Deficiency, +3 more
- Locations
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- University of California San Francisco San Francisco, California, United States
- Children's National Health System Washington D.C., District of Columbia, United States
- University of South Florida Tampa, Florida, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States