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Conditions
Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +21 more
Locations
  • University of California Los Angeles Los Angeles, California, United States
  • Lucile Packard Children's Hospital at Stanford Palo Alto, California, United States
  • The Children's Hospital of Colorado Aurora, Colorado, United States
  • Children's National Medical Center Washington D.C., District of Columbia, United States
Conditions
Amino Acid Metabolism, Inborn Errors, Argininosuccinic Aciduria, Brain Diseases, +31 more
Locations
  • Children's National Medical Center Washington D.C., District of Columbia, United States
  • Columbia University, Morgan Stanley Children's Hospital New York, United States
  • Medical College Wisconsin Milwaukee, Wisconsin, United States

NCT03655223

Conditions
17 Alpha-Hydroxylase Deficiency, 3-Hydroxy-3-Methylglutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, +456 more
Locations
  • RTI International Research Triangle Park, North Carolina, United States