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Recruiting
The Myelin Disorders Biorepository Project
NCT03047369
- Conditions
- 4H Syndrome, ADLD, AGS, +173 more
- Locations
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- Children's Hospital of Los Angeles Los Angeles, California, United States
- Children's Hospital of Orange County Orange, California, United States
- Stanford University (Lucile Packard Children's Hospital) Palo Alto, California, United States
- University of California, Davis (UC Davis Health) Sacramento, California, United States
NCT02699190
- Conditions
- 4H Syndrome, ADLD, AGS, +173 more
- Locations
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- The Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
NCT04270682
- Conditions
- CTX, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +7 more
- Locations
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- Travere Investigational Site Aurora, Colorado, United States
- Travere Investigational Site Orlando, Florida, United States
- Travere Investigational Site Iowa City, Iowa, United States
- Travere Investigational Site New Orleans, Louisiana, United States