Completed A Safety, Tolerability, and Efficacy Study of BMN 190 in Pediatric Patients < 18 Years of Age With CLN2 Disease NCT02678689 Conditions Batten Disease, CLN2 Disease, CLN2 Disorder, +14 more Locations Nationwide Children's Hospital — Columbus, Ohio, United States Universitaetsklinikum Hamburg-Eppendorf — Hamburg, Germany Children's Hospital Bambino Gesù,IRCCS — Rome, Piazza, Italy Great Ormond Street Childrens Hospital — London, United Kingdom View Trial Details
Completed An Extension Study to Evaluate the Long-Term Efficacy and Safety of BMN 190 in Patients With CLN2 Disease NCT02485899 Conditions Batten Disease, CLN2 Disease, CLN2 Disorder, +14 more Locations Nationwide Children's Hospital — Columbus, Ohio, United States Universitaetsklinikum Hamburg-Eppendorf — Hamburg, Germany Children's Hospital Bambino Gesù,IRCCS — Rome, Piazza, Italy Great Ormond Street Childrens Hospital — London, United Kingdom View Trial Details