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NCT07723248
- Conditions
- Bulbo-Spinal Atrophy, X-Linked, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +24 more
- Locations
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- Urology Specialists of the Carolinas - University Place Charlotte, North Carolina, United States
- Summit Urology Murray, Utah, United States
NCT06764485
- Conditions
- Bulbo-Spinal Atrophy, X-Linked, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +20 more
- Locations
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- Central Alabama Research Birmingham, Alabama, United States
- Banner MD Anderson Cancer Center Gilbert, Arizona, United States
- Local Institution - 0370 Anaheim, California, United States
- Moores Cancer Center La Jolla, California, United States
NCT04708431
- Conditions
- Androgen Insensitivity Syndrome, Androgen-Insensitivity Syndrome, Bulbo-Spinal Atrophy, X-Linked, +24 more
- Locations
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- National Institutes of Health Clinical Center Bethesda, Maryland, United States
NCT07336446
- Conditions
- Bulbo-Spinal Atrophy, X-Linked, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +20 more
- Locations
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- Research Site Duarte, California, United States
- Research Site San Francisco, California, United States
- Research Site Tampa, Florida, United States
- Research Site Boston, Massachusetts, United States
- Conditions
- Bulbo-Spinal Atrophy, X-Linked, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +10 more
- Locations
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- Univ of Alabama at Birmingham Birmingham, Alabama, United States
- Uni Of Iowa Hospitals And Clinics Iowa City, Iowa, United States
- University of Kansas Cancer Center Westwood, Kansas, United States
- Wichita Urology Group PA Wichita, Kansas, United States
NCT05966038
- Conditions
- ALS, Amyotrophic Lateral Sclerosis, Bulbar Palsy, Progressive, +21 more
- Locations
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- Loma Linda University Health Loma Linda, California, United States
- Kaiser Permanente Los Angeles, California, United States
- University of Florida Gainesville, Florida, United States
- Northwestern University Chicago, Illinois, United States
NCT06365788
- Conditions
- Breast Diseases, Breast Neoplasms, Bulbo-Spinal Atrophy, X-Linked, +16 more
- Locations
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- ZAS Augustinus Antwerp, Belgium
- Antwerp University Hospital Antwerp, Belgium
- University Hospital Brussels Brussels, Belgium
- Ghent University Hospital Ghent, Belgium
NCT04944940
- Conditions
- Bulbo-Spinal Atrophy, X-Linked, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +11 more
- Locations
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- National Institutes of Health Clinical Center Bethesda, Maryland, United States
Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
NCT01793168
- Conditions
- 1p36 Deletion Syndrome, 3-Methylglutaconic Aciduria, Type V, 4p Deletion Syndrome, Non-Wolf-Hirschhorn Syndrome, +698 more
- Locations
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- Sanford Health Sioux Falls, South Dakota, United States
- Online Patient Enrollment System Sydney, Australia
NCT06862596
- Conditions
- Bulbo-Spinal Atrophy, X-Linked, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +10 more
- Locations
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- Tokyo University Hospital Bunkyō City, Japan
- Chiba University Hospital Chiba, Japan
- Hokkaido University Hospital Sapporo, Japan
- Jichi Medical University Hospital Shimotsuke, Japan
UK SMA Patient Registry
NCT04292574
- Conditions
- Bulbo-Spinal Atrophy, X-Linked, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
- Locations
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- John Walton Muscular Dystrophy Research Centre Newcastle upon Tyne, United Kingdom
NCT06169046
- Conditions
- Bulbo-Spinal Atrophy, X-Linked, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +10 more
- Locations
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- Azienda Ospedale Università di Padova Padova, PD, Italy
NCT03555578
- Conditions
- Bulbo-Spinal Atrophy, X-Linked, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +10 more
- Locations
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- Takeda Selected Site Tokyo, Japan
Darolutamide in Patients With Androgen Receptor-Positive Salivary Gland Carcinoma (DISCOVARY)
NCT05694819
- Conditions
- Bulbo-Spinal Atrophy, X-Linked, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +18 more
- Locations
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- Nagoya University Hospital Nagoya, Aichi-ken, Japan
- Chiba University Hospital Chiba, Japan
- National Cancer Center Hospital East Kashiwa, Chiba, Japan
- National Hospital Organization Kyushu Medical Center Fukuoka, Japan
NCT06411912
- Conditions
- Bulbo-Spinal Atrophy, X-Linked, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +11 more
- Locations
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- Rigshospitalet, Klinik for Nerve- og Muskelsygdomme & Copenhagen Neuromuscular Center Copenhagen, Denmark
- IRCCS Istituto Neurologico Carlo Besta Milan, Italy
- Azienda Ospedale Università di Padova Padova, Italy
- Kyungpook National University Chilgok Hospital Daegu, South Korea
- Conditions
- Atrophy, Bulbo-Spinal Atrophy, X-Linked, Central Nervous System Diseases, +19 more
- Locations
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- Boston Childrens Hospital Boston, Massachusetts, United States
- Child Hosp Of The Kings Daughters Norfolk, Virginia, United States
- University of Wisconsin Madison Medical School Madison, Wisconsin, United States
- Novartis Investigative Site Parkville, Victoria, Australia
NCT02294461
- Conditions
- Bulbo-Spinal Atrophy, X-Linked, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +20 more
- Locations
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- CN00103 Beijing, China
- CN00104 Beijing, China
- CN00106 Beijing, China
- CN00111 Beijing, China
Patients With ALS and Other Motor Disorders Will be Treated With Mesenchymal Cell Exosome Solution
NCT07105371
- Conditions
- Basal Ganglia Diseases, Brain Diseases, Bulbo-Spinal Atrophy, X-Linked, +21 more
- Locations
-
- Medical Surgical Associates Center St John's, Antigua and Barbuda
NCT01969578
- Conditions
- Adenocarcinoma, Bulbo-Spinal Atrophy, X-Linked, Carcinoma, +22 more
- Locations
-
- Medical University Vienna - General Hospital AKH Vienna, Austria
- ZNA Middelheim Antwerp, Belgium
- Hopitaux Universitaires Bordet-Erasme - Institut Jules Bordet Brussels, Belgium
- Cliniques Universitaires Saint-Luc Brussels, Belgium
NCT04851873
- Conditions
- Atrophy, Bulbo-Spinal Atrophy, X-Linked, Central Nervous System Diseases, +19 more
- Locations
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- Novartis Investigative Site Boston, Massachusetts, United States
- Novartis Investigative Site St Louis, Missouri, United States
- Novartis Investigative Site Randwick, New South Wales, Australia
- Novartis Investigative Site Leuven, Belgium