Recruiting ASXL-Related Disorders Natural History Study NCT03303716 Conditions ASXL1 Gene Mutation, ASXL2 Gene Mutation, ASXL3 Gene Mutation, +4 more Locations University of California, Los Angeles — Los Angeles, California, United States View Trial Details
Recruiting Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford NCT01793168 Conditions 1p36 Deletion Syndrome, 3-Methylglutaconic Aciduria, Type V, 4p Deletion Syndrome, Non-Wolf-Hirschhorn Syndrome, +698 more Locations Sanford Health — Sioux Falls, South Dakota, United States Online Patient Enrollment System — Sydney, Australia View Trial Details