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Published and searchable clinical trials
NCT03937817
- Conditions
- Alpha and Beta Thalassemia, Anemia, Anemia, Hemolytic, +17 more
- Locations
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- National Institutes of Health Clinical Center Bethesda, Maryland, United States
NCT07599176
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +10 more
- Locations
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- National Institutes of Health Clinical Center Bethesda, Maryland, United States
Study of Safety & PK of Luspatercept (ACE-536) in Pediatric Participants With Beta (β)-Thalassemia
NCT04143724
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +8 more
- Locations
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- Local Institution - 601 Los Angeles, California, United States
- New York Presbyterian Hospital New York, United States
- Southern Medical University Nanfang Hospital Guangzhou, Guangdong, China
- Shenzhen Second People's Hospital Shenzhen, Guangdong, China
NCT03653338
- Conditions
- Anemia, Anemia, Aplastic, Anemia, Diamond-Blackfan, +18 more
- Locations
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- Children's Hospital of Pittsburgh of UPMC Pittsburgh, Pennsylvania, United States
NCT04064060
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +13 more
- Locations
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- Local Institution - 968 Los Angeles, California, United States
- Local Institution - 971 Oakland, California, United States
- Local Institution - 978 Stanford, California, United States
- Local Institution - 975 Tampa, Florida, United States
NCT05736419
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +10 more
- Locations
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- Memorial Sloan Kettering at Basking Ridge (Consent only) Basking Ridge, New Jersey, United States
- Memorial Sloan Kettering Monmouth (Consent only) Middletown, New Jersey, United States
- Memorial Sloan Kettering Bergen (Consent only) Montvale, New Jersey, United States
- Memorial Sloan Kettering Suffolk - Commack (Consent only) Commack, New York, United States
NCT06364774
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +8 more
- Locations
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- Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
NCT05735717
- Conditions
- AML, Acute Leukemia, Acute Lymphoblastic Leukemia, +74 more
- Locations
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- University of Minnesota Masonic Cancer Center Minneapolis, Minnesota, United States
NCT05477563
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +11 more
- Locations
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- New York Presbyterian Hospital - Morgan Stanley Children's Hospital New York, United States
- Levine Children's Hospital - Hematology Charlotte, North Carolina, United States
- TriStar Medical Group Children's Specialists - Pediatric Oncology Nashville, Tennessee, United States
- University Hospital Dusseldorf - Department of Pediatric Oncology, Hematology and Clinical Immunology Düsseldorf, Germany
NCT06647979
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +12 more
- Locations
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- Boston Children's Hospital Boston, Massachusetts, United States
NCT04528355
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +119 more
- Locations
-
- UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
NCT01245179
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +9 more
- Locations
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- Augusta University Augusta, Georgia, United States
NCT01962415
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +125 more
- Locations
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- UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
NCT04099966
- Conditions
- Acute Leukemia, Amegakaryocytic Thrombocytopenia, Anemia, +34 more
- Locations
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- New York Medical College Valhalla, New York, United States
NCT06271512
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +8 more
- Locations
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- UCSF Benioff Children's Hospitals Oakland, California, United States
- Stanford University Palo Alto, California, United States
- University of Minnesota Minneapolis, Minnesota, United States
- Cohen Children's Medical Center New Hyde Park, New York, United States
NCT06539169
- Conditions
- Alpha-Thalassemia, Alzheimer Disease, Amyloidosis, +104 more
- Locations
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- xCures Los Altos, California, United States
NCT05799118
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +12 more
- Locations
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- Boston Children's Hospital Boston, Massachusetts, United States
- Lucrecia Paím Maternity Luanda, Angola
- University of Buenos Aires Buenos Aires, Argentina
- University Hospitals Leuven Leuven, Belgium
Open-Label Extension Study to Pioneer Study 6058-SCD-101
NCT07401823
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +9 more
- Locations
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- University of Arkansas for Medical Sciences Little Rock, Arkansas, United States
- University of California, Los Angeles Los Angeles, California, United States
- Our Lady of the Lake Hospital Baton Rouge, Louisiana, United States
- Boston Medical Center Boston, Massachusetts, United States
A Long-term Follow-up Study in Participants Who Received CTX001
NCT04208529
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +11 more
- Locations
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- Lucile Packard Children's Hospital Palo Alto, California, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago - Hematology Chicago, Illinois, United States
- Herbert Irving Pavilion - Hematology New York, United States
- New York Presbyterian Hospital - Morgan Stanley Children's Hospital New York, United States
The BENeFiTS Trial in Beta Thalassemia Intermedia
NCT04432623
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +10 more
- Locations
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- UCSF Benioff Children's Hospital at Oakland Oakland, California, United States
- Massachusetts General Hospital Boston, Massachusetts, United States
- Susan Perrine Weston, Massachusetts, United States
- Weil Cornell Medicine New York, United States