Clinical trial discovery
Find Clinical Trials
Search studies by condition, treatment, location, eligibility, or trial identifier.
Showing 1–20 of 21 trials
Active filters
Clinical trials found
Published and searchable clinical trials
NCT02435940
- Conditions
- Abetalipoproteinemia, Abnormalities, Multiple, Achromatopsia, +100 more
- Locations
-
- Foundation Fighting Blindness Columbia, Maryland, United States
NCT03307304
- Conditions
- Batten Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +11 more
- Locations
-
- National Institutes of Health Clinical Center Bethesda, Maryland, United States
NCT03333200
- Conditions
- ALD, Alpha-Mannosidosis, Batten Disease, +78 more
- Locations
-
- UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
NCT01873924
- Conditions
- Batten Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +19 more
- Locations
-
- University of Rochester Rochester, New York, United States
NCT02254863
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +55 more
- Locations
-
- Duke University Medical Center Durham, North Carolina, United States
NYSCF Scientific Discovery Biobank
NCT06203106
- Conditions
- ALS, Adnexal Diseases, Alzheimer Disease, +101 more
- Locations
-
- New York Stem Cell Foundation Research Institute New York, United States
Examining Developmental Outcomes of Children Diagnosed With CLN2 Disease
NCT03862274
- Conditions
- Batten Disease, CLN2, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +11 more
- Locations
-
- Nationwide Children's Hospital Columbus, Ohio, United States
Gene Therapy Trial for CLN6 Batten Disease
NCT07582484
- Conditions
- Batten Disease, Batten's Disease, CLN6, +14 more
- Locations
-
- University of California, San Diego - Rady Children's La Jolla, California, United States
NCT05174039
- Conditions
- Batten Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +10 more
- Locations
-
- Texas Children Hospital Houston, Texas, United States
NCT02678689
- Conditions
- Batten Disease, CLN2 Disease, CLN2 Disorder, +14 more
- Locations
-
- Nationwide Children's Hospital Columbus, Ohio, United States
- Universitaetsklinikum Hamburg-Eppendorf Hamburg, Germany
- Children's Hospital Bambino Gesù,IRCCS Rome, Piazza, Italy
- Great Ormond Street Childrens Hospital London, United Kingdom
NCT01586455
- Conditions
- Acute Lymphocytic Leukemia, Acute Myelogenous Leukemia, Adrenal Gland Diseases, +84 more
- Locations
-
- Children's Hospital Colorado Denver, Colorado, United States
- New York Medical College Valhalla, New York, United States
- University of Utah Salt Lake City, Utah, United States
NCT02485899
- Conditions
- Batten Disease, CLN2 Disease, CLN2 Disorder, +14 more
- Locations
-
- Nationwide Children's Hospital Columbus, Ohio, United States
- Universitaetsklinikum Hamburg-Eppendorf Hamburg, Germany
- Children's Hospital Bambino Gesù,IRCCS Rome, Piazza, Italy
- Great Ormond Street Childrens Hospital London, United Kingdom
NCT01161576
- Conditions
- Batten Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +11 more
- Locations
-
- Weill Cornell Medical College New York, United States
NCT01414985
- Conditions
- Batten Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +11 more
- Locations
-
- Weill Cornell Medical College New York, United States
NCT01035424
- Conditions
- Batten Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +11 more
- Locations
-
- Weill Cornell Medicine New York, United States
NCT00151216
- Conditions
- Batten Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +11 more
- Locations
-
- New York Presbyterian Hospital - Weill Medical College of Cornell University New York, United States
- Conditions
- Batten Disease, CLN2 Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
- Locations
-
- Nationwide Children's Hospital Columbus, Ohio, United States
- University Hamburg-Eppendorf Hamburg, Germany
- Bambino Gesù Children's Hospital Rome, Italy
- Guy's & St. Thomas NHS Foundation Trust London, United Kingdom
NCT00176904
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +55 more
- Locations
-
- Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States
Gene Therapy for Children With CLN3 Batten Disease
NCT03770572
- Conditions
- Batten Disease, CLN3, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +11 more
- Locations
-
- Nationwide Children's Hospital Columbus, Ohio, United States
Long-Term Follow Up of CLN6 Batten Disease Subjects Following Gene Transfer
NCT04273243
- Conditions
- Batten Disease, CLN6, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +11 more
- Locations
-
- Nationwide Children's Hosptial Columbus, Ohio, United States