Recruiting Real-World Effects of MC4R Agonist Therapy in BBS and Severe Genetic Obesity NCT07674290 Conditions Abnormalities, Multiple, Alstrom Syndrome, Bardet Biedl Syndrome, +25 more Locations University Hospital Essen, Deparment of Pediatrics II — Essen, Germany View Trial Details
Recruiting ARPKD Database Study NCT01401998 Conditions Abnormalities, Multiple, Agenesis of Cerebellar Vermis, Autosomal Recessive Polycystic Kidney Disease, +39 more Locations Children's National Hospital — Washington D.C., District of Columbia, United States Emory — Atlanta, Georgia, United States Boston Children's — Boston, Massachusetts, United States Cincinnati Children's — Cincinnati, Ohio, United States View more locations Show fewer locations Loading locations... View Trial Details
Recruiting GROWing Up With Rare GENEtic Syndromes NCT04463316 Conditions 17p- Deletiesyndrome, 1q25-32 Deletie, 22q11 Deletion Syndrome, +138 more Locations Erasmus Medical Center — Rotterdam, South Holland, Netherlands View Trial Details