Recruiting ASXL-Related Disorders Natural History Study NCT03303716 Conditions ASXL1 Gene Mutation, ASXL2 Gene Mutation, ASXL3 Gene Mutation, +4 more Locations University of California, Los Angeles — Los Angeles, California, United States View Trial Details
Active, Not Recruiting Personalized Antisense Oligonucleotide Therapy for A Single Participant With ASXL3 Gene Mutation NCT07197268 Conditions Bainbridge-Ropers Syndrome Locations University of North Carolina Chapel Hill — Chapel Hill, North Carolina, United States View Trial Details