Recruiting Safety of Single and Repeat Dose of PYC-001 Eye Injections in People With Autosomal Dominant Optic Atrophy (Myrtle) NCT06970106 Conditions Autosomal Dominant Optic Atrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cranial Nerve Diseases, +16 more Locations Save Sight Institute - Sydney Eye Hospital — Sydney, New South Wales, Australia Cerulea Clinical Trials — East Melbourne, Australia Retina Specialists — Auckland, New Zealand View Trial Details
Recruiting Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford NCT01793168 Conditions 1p36 Deletion Syndrome, 3-Methylglutaconic Aciduria, Type V, 4p Deletion Syndrome, Non-Wolf-Hirschhorn Syndrome, +698 more Locations Sanford Health — Sioux Falls, South Dakota, United States Online Patient Enrollment System — Sydney, Australia View Trial Details
Active, Not Recruiting SAD of IVT PYC-001 in OPA1 Mutation-Associated Autosomal Dominant Optic Atrophy (Sundew) NCT06461286 Conditions Autosomal Dominant Optic Atrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cranial Nerve Diseases, +16 more Locations Save Sight Institute - Sydney Eye Hospital — Sydney, New South Wales, Australia Center for Eye Research Australia (CERA) — East Melbourne, Victoria, Australia View Trial Details
